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Hacein-Bey-Abina, S; Pai, SY; Gaspar, HB; Armant, M; Berry, CC; Blanche, S; Bleesing, J; Blondeau, J; De Boer, H; Buckland, KF; Caccavelli, L; Cros, G; De Oliveira, S; Fernández, KS; Guo, D; Harris, CE; Hopkins, G; Lehmann, LE; Lim, A; London, WB; Van Der Loo, JCM; Malani, N; Male, F; Malik, P; Marinovic, MA; McNicol, AM; Moshous, D; Neven, B; Oleastro, M; Picard, C; Ritz, J; Rivat, C; Schambach, A; Shaw, KL; Sherman, EA; Silberstein, LE; Six, E; Touzot, F; Tsytsykova, A; Xu-Bayford, J; Baum, C; Bushman, FD; Fischer, A; Kohn, DB; Filipovich, AH; Notarangelo, LD; Cavazzana, M; Williams, DA; Thrasher, AJ
New England Journal of Medicine. 371(15)
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[AR] Sherman, EA
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