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Academic Journal
Kirschner, J; Bernert, G; Butoianu, N; De Waele, L; Fattal-Valevski, A; Haberlova, J; Moreno, T; Klein, A; Kostera-Pruszczyk, A; Mercuri, E; Quijano-Roy, S; Sejersen, T; Tizzano, EF; van der Pol, WL; Wallace, S; Zafeiriou, D; Ziegler, A; Muntoni, F; Servais, L
European journal of paediatric neurology : EJPN : official journal of the European Paediatric Neurology Society. 51:73-78
Academic Journal
Edel, L; Grime, C; Robinson, V; Manzur, A; Abel, F; Munot, P; Ridout, D; Scoto, M; Muntoni, F; Chan, E
In Neuromuscular Disorders April 2021 31(4):300-309
Academic Journal
McDonald, CM; Muntoni, F; Penematsa, V; Jiang, J; Kristensen, A; Bibbiani, F; Goodwin, E; Gordish-Dressman, H; Morgenroth, L; Werner, C; Li, J; Able, R; Trifillis, P; Tulinius, M
Journal of comparative effectiveness research. 11(3):139-155
Academic Journal
Campbell, C; Barohn, RJ; Bertini, E; Chabrol, B; Comi, GP; Darras, BT; Finkel, RS; Flanigan, KM; Goemans, N; Iannaccone, ST; Jones, KJ; Kirschner, J; Mah, JK; Mathews, KD; McDonald, CM; Mercuri, E; Nevo, Y; Pereon, Y; Ben Renfroe, J; Ryan, MM; Sampson, JB; Schara, U; Sejersen, T; Selby, K; Tulinius, M; Vilchez, JJ; Voit, T; Wei, LJ; Wong, BL; Elfring, G; Souza, M; McIntosh, J; Trifillis, P; Peltz, SW; Muntoni, F
Journal of comparative effectiveness research. 9(14):973-984
Academic Journal
Kirschner, J; Butoianu, N; Goemans, N; Haberlova, J; Kostera-Pruszczyk, A; Mercuri, E; van der Pol, WL; Quijano-Roy, S; Sejersen, T; Tizzano, EF; Ziegler, A; Servais, L; Muntoni, F
European journal of paediatric neurology : EJPN : official journal of the European Paediatric Neurology Society. 28:38-43
Academic Journal
Thangarajh, M; Elfring, GL; Trifillis, P; McIntosh, J; Peitz, SW; Ryan, MM; Kornberg, AJ; RodriguezCasero, V; Wray, A; Jones, KJ; North, K; Goemans, N; Buyse, GM; Campbell, C; Mah, J; Sarnat, H; Selby, K; Voit, T; Doppler, V; De Castro, D; Chabrol, B; Levy, N; Halbert, C; Pereon, Y; Magot, A; Perrier, J; Mahe, JY; Schara, U; Lutz, S; Busse, M; Della Marina, A; Kirschner, J; Stanescu, A; Pohl, A; RensingZimmerman, C; Bertini, E; D'Amico, A; Kofler, A; Carlesi, A; Bonetti, AM; Santecchia, L; Emma, F; Bergami, G; Mercuri, EM; Vasco, G; Bianco, F; Mazzone, ES; De Sanctis, R; Alfieri, P; Pane, M; Messina, S; Comi, GP; Magri, F; Lucchini, V; Corti, SP; Moggio, MG; Sciacco, M; Bresolin, N; Prelle, AC; Magri, R; Virgilio, R; Lamperti, C; Nevo, Y; DorWollman, T; Vilchez, J; Muelas, N; Sevilla, T; Smeyers, P; de la Osa, A; Colomer, J; Ortez, CI; Nascimento, A; Febrer, A; Medina, J; Tulinus, M; Thorarinsdottir, B; Darin, N; Sejersen, T; Hovmoller, M; Bushby, K; Straub, V; Guglieri, M; Sarkozy, A; Willis, T; Eagle, M; Mayhew, A; Muntoni, F; Cirak, S; Manzur, AY; Robb, SA; Kinali, M; Quinlivan, RCM; Smith, MR; Pandey, R; Wong, B; Collins, J; Finkel, R; Bonnemann, C; Yang, M; Foley, AR; Yum, S; Sampson, J; Bromberg, M; Swoboda, K; Day, J; Karachunski, P; Mathews, K; Bonthius, D; Laubenthal, KS; Darras, B; Kang, P; Parson, J; Barohn, R; Dasouki, M; Anderson, H; Burns, J; Dimachkie, M; Pasnoor, M; Wang, YX; Ciafaloni, E; Heatwole, C; Connolly, A; Pestronk, A; Al-Lozi, M; Lopate, G; Golumbek, P; Sommerville, B; Wang, L; Wojcicka-Mitchell, A; Godbey, A; Harms, M; Varadachary, A; Iyadurai, S; Rojas, L; Iannacone, S; Khonghatithum, C; Sproule, D; De Vivo, D; Constantinescu, A; McDonald, C; Han, J; Ben Renfroe; Russman, B; Sussman, M; BurnsWechsler, S; Juel, V; Hobson-Webb, L; Smith, E
Neurology. 91(13):E1215-E1219
Academic Journal
Finkel, RS; Mercuri, E; Meyer, OH; Simonds, AK; Schroth, MK; Graham, RJ; Kirschner, J; Iannaccone, ST; Crawford, TO; Woods, S; Muntoni, F; Wirth, B; Montes, J; Main, M; Mazzone, ES; Vitale, M; Snyder, B; Quijano-Roy, S; Bertini, E; Davis, RH; Qian, Y; Sejersen, T
Neuromuscular disorders : NMD. 28(3):197-207
Academic Journal
Mercuri, E; Finkel, RS; Muntoni, F; Wirth, B; Montes, J; Main, M; Mazzone, ES; Vitale, M; Snyder, B; Quijano-Roy, S; Bertini, E; Davis, RH; Meyer, OH; Simonds, AK; Schroth, MK; Graham, RJ; Kirschner, J; Iannaccone, ST; Crawford, TO; Woods, S; Qian, Y; Sejersen, T
Neuromuscular disorders : NMD. 28(2):103-115
Academic Journal
In Value in Health January 2022 25(1) Supplement:S218-S218
Periodical
Mendell, JR; Muntoni, F; McDonald, CM; Mercuri, EM; Ciafaloni, E; Komaki, H; Leon-Astudillo, C; Nascimento, A; Proud, C; Schara-Schmidt, U; Veerapandiyan, A; Zaidman, CM; Guridi, M; Murphy, AP; Reid, C; Wandel, C; Darton, E; Mason, S; Potter, RA; Singh, T; Zhang, W; Fontoura, P; Elkins, JS; Rodino-Klapac, LR
The Canadian Journal of Neurological Sciences; June 2024, Vol. 51 Issue: Supplement 1 pS9-S10, 2p
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