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Academic Journal
Rachael A. Potter; Ellyn L. Peterson; Danielle Griffin; Grace Cooper Olson; Sarah Lewis; Kyle Cochran; Jerry R. Mendell; Louise R. Rodino-Klapac
Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101195- (2024)
Academic Journal
Alexa C. Klimchak; Lauren E. Sedita; Louise R. Rodino-Klapac; Jerry R. Mendell; Craig M. McDonald; Katherine L. Gooch; Daniel C. Malone
Journal of Market Access & Health Policy, Vol 11, Iss 1 (2023)
Academic Journal
Rachael A. Potter; Danielle A. Griffin; Kristin N. Heller; Jerry R. Mendell; Louise R. Rodino-Klapac
Biology Open, Vol 12, Iss 9 (2023)
Academic Journal
Ursula Moore; Ericky Caldas de Almeida Araújo; Harmen Reyngoudt; Heather Gordish‐Dressman; Fiona E. Smith; Ian Wilson; Meredith James; Anna Mayhew; Laura Rufibach; John W. Day; Kristi J. Jones; Diana X. Bharucha‐Goebel; Emmanuelle Salort‐Campana; Alan Pestronk; Maggie C. Walter; Carmen Paradas; Tanya Stojkovic; Madoka Mori‐Yoshimura; Elena Bravver; Elena Pegoraro; Jerry R. Mendell; The Jain COS Consortium; Kate Bushby; Andrew M. Blamire; Volker Straub; Pierre G. Carlier; Jordi Diaz‐Manera
Journal of Cachexia, Sarcopenia and Muscle, Vol 13, Iss 6, Pp 2888-2897 (2022)
Academic Journal
Jerry R. Mendell; Perry B. Shieh; Craig M. McDonald; Zarife Sahenk; Kelly J. Lehman; Linda P. Lowes; Natalie F. Reash; Megan A. Iammarino; Lindsay N. Alfano; Brenna Sabo; Jeremy D. Woods; Christy L. Skura; Howard C. Mao; Loretta A. Staudt; Danielle A. Griffin; Sarah Lewis; Shufang Wang; Rachael A. Potter; Teji Singh; Louise R. Rodino-Klapac
Frontiers in Cell and Developmental Biology, Vol 11 (2023)
Academic Journal
Jerry R. Mendell; Anne M. Connolly; Kelly J. Lehman; Danielle A. Griffin; Sohrab Z. Khan; Sachi D. Dharia; Lucía Quintana-Gallardo; Louise R. Rodino-Klapac
Molecular Therapy: Methods & Clinical Development, Vol 25, Iss , Pp 74-83 (2022)
Academic Journal
Erin O’Rourke; Jerry R. Mendell; Zarife Sahenk; Kelly J. Lehman; Linda P. Lowes; Natalie F. Reash; Megan Iammarino; Lindsay Alfano; Sarah Lewis; Kathleen Church; Richard Shell; Rachael A. Potter; Danielle Griffin; Mark J. Hogan; Shufang Wang; Stefanie Mason; Eddie Darton; Louise Rodino-Klapac
Genetics in Medicine Open, Vol 1, Iss 1, Pp 100342- (2023)
Academic Journal
Zarife Sahenk; Burcak Ozes; Darren Murrey; Morgan Myers; Kyle Moss; Mehmet E. Yalvac; Alicia Ridgley; Lei Chen; Jerry R. Mendell
Molecular Therapy: Methods & Clinical Development, Vol 22, Iss , Pp 401-414 (2021)
Academic Journal
John W. Day; Richard S. Finkel; Eugenio Mercuri; Kathryn J. Swoboda; Melissa Menier; Rudolf van Olden; Sitra Tauscher-Wisniewski; Jerry R. Mendell
Molecular Therapy: Methods & Clinical Development, Vol 21, Iss , Pp 76-82 (2021)
Academic Journal
Anna G. Mayhew; Meredith K. James; Ursula Moore; Helen Sutherland; Marni Jacobs; Jia Feng; Linda Pax Lowes; Lindsay N. Alfano; Robert Muni Lofra; Laura E. Rufibach; Kristy Rose; Tina Duong; Luca Bello; Irene Pedrosa-Hernández; Scott Holsten; Chikako Sakamoto; Aurélie Canal; Nieves Sánchez-Aguilera Práxedes; Simone Thiele; Catherine Siener; Bruno Vandevelde; Brittney DeWolf; Elke Maron; Heather Gordish-Dressman; Heather Hilsden; Michela Guglieri; Jean-Yves Hogrel; Andrew M. Blamire; Pierre G. Carlier; Simone Spuler; John W. Day; Kristi J. Jones; Diana X. Bharucha-Goebel; Emmanuelle Salort-Campana; Alan Pestronk; Maggie C. Walter; Carmen Paradas; Tanya Stojkovic; Madoka Mori-Yoshimura; Elena Bravver; Jordi Díaz-Manera; Elena Pegoraro; Jerry R. Mendell; Volker Straub
Frontiers in Neurology, Vol 13 (2022)
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[AR] Jerry R. Mendell
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