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Hillen, Anne E J; Hruzova, Martina; Rothgangl, Tanja; Breur, Marjolein; Bugiani, Marianna; van der Knaap, Marjo S; Schwank, Gerald; Heine, Vivi M (2022). In vivo targeting of a variant causing vanishing white matter using CRISPR/Cas9. Molecular Therapy - Methods & Clinical Development, 25:17-25.
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Annals of Clinical and Translational Neurology vol.5 (2018) p.429-444 [ISSN 2328-9503]
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[AR] Heine, Vivi M
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