부산대학교 도서관

Ferrua, F; Galimberti, S; Courteille, V; Slatter, MA; Booth, C; Moshous, D; Neven, B; Blanche, S; Cavazzana, M; Laberko, A

JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY. 143(6):2238-2253

Galgano, D; Soheili, T; Voss, M; Torralba-Raga, L; Tesi, B; Cichocki, F; Andre, I; Rettig, J; Cavazzana, M; Bryceson, Y

FRONTIERS IN IMMUNOLOGY. 11

Rivière, J; Hauer, J; Poirot, L; Brochet, J; Souque, P; Mollier, K; Gouble, A; Charneau, P; Fischer, A; Pâques, F; de Villartay, J-P; Cavazzana, M

Gene Therapy. May2014, Vol. 21 Issue 5, p529-532. 4p.

Daniela Cesana; Maria Pia Cicalese; Andrea Calabria; Pietro Merli; Roberta Caruso; Monica Volpin; Laura Rudilosso; Maddalena Migliavacca; Federica Barzaghi; Claudia Fossati; Francesco Gazzo; Simone Pizzi; Andrea Ciolfi; Alessandro Bruselles; Francesca Tucci; Giulio Spinozzi; Giulia Pais; Fabrizio Benedicenti; Matteo Barcella; Ivan Merelli; Pierangela Gallina; Stefania Giannelli; Francesca Dionisio; Serena Scala; Miriam Casiraghi; Luisa Strocchio; Luciana Vinti; Lucia Pacillo; Eleonora Draghi; Marcella Cesana; Sara Riccardo; Chiara Colantuono; Emmanuelle Six; Marina Cavazzana; Filippo Carlucci; Manfred Schmidt; Caterina Cancrini; Fabio Ciceri; Luca Vago; Davide Cacchiarelli; Bernhard Gentner; Luigi Naldini; Marco Tartaglia; Eugenio Montini; Franco Locatelli; Alessandro Aiuti

Nat Commun
Nature Communications, Vol 15, Iss 1, Pp 1-18 (2024)

Ramadier, Sophie; Chalumeau, Anne; Felix, Tristan; Othman, Nadia; Aknoun, Sherazade; Casini, Antonio; Maule, Giulia; Masson, Cecile; de Cian, Anne; Frati, Giacomo; Brusson, Megane; Concordet, Jean-Paul; Cavazzana, Marina; Cereseto, Anna; El Nemer, Wassim; Amendola, Mario; Wattellier, Benoit; Meneghini, Vasco; Miccio, Annarita

Molecular Therapy. 30:145-163

Delville, Marianne; Bellier, Florence; Leon, Juliette; Klifa, Roman; Lizot, Sabrina; Vinçon, Hélène; Sobrino, Steicy; Thouenon, Romane; Marchal, Armance; Garrigue, Alexandrine; Olivré, Juliette; Charbonnier, Soëli; Lagresle-Peyrou, Chantal; Amendola, Mario; Schambach, Axel; Gross, David; Lamarthée, Baptiste; Benoist, Christophe; Zuber, Julien; Andre, Isabelle; Cavazzana, Marina; Six, Emmanuelle

Blood. 137:2326-2336

Nieves Diaz; Maria Juarez; Caterina Cancrini; Maximilian Heeg; Pere Soler-Palacín; Andrew Payne; Geoffrey I Johnston; Eric Helmer; Dionne Cain; Joanne Mann; Daisy Yuill; Francesca Conti; Silvia Di Cesare; Stephan Ehl; Marina Garcia-Prat; Maria Elena Maccari; Andrea Martín-Nalda; Mónica Martínez-Gallo; Despina Moshous; Veronica Santilli; Michaela Semeraro; Alessandra Simonetti; Felipe Suarez; Marina Cavazzana; Sven Kracker

The Journal of Immunology. 205:2979-2987

Antoniani, Chiara; Meneghini, Vasco; Lattanzi, Annalisa; Felix, Tristan; Romano, Oriana; Magrin, Elisa; Weber, Leslie; Pavani, Giulia; El Hoss, Sara; Kurita, Ryo; Nakamura, Yukio; Cradick, Thomas; Lundberg, Ante; Porteus, Matthew; Amendola, Mario; El Nemer, Wassim; Cavazzana, Marina; Mavilio, Fulvio; Miccio, Annarita

Blood

Rivera-Munoz, P; Abramowski, V; Jacquot, S; André, P; Charrier, S; Lipson-Ruffert, K; Fischer, A; Galy, A; Cavazzana, M; de Villartay, J-P

Gene Therapy. Feb 01, 2016 23(2):176-186

Maria Elena Maccari; Martin Wolkewitz; Charlotte Schwab; Tiziana Lorenzini; Jennifer W. Leiding; Nathalie Aladjdi; Hassan Abolhassani; Wadih Abou-Chahla; Alessandro Aiuti; Saba Azarnoush; Safa Baris; Vincent Barlogis; Federica Barzaghi; Ulrich Baumann; Marketa Bloomfield; Nadezda Bohynikova; Damien Bodet; David Boutboul; Giorgia Bucciol; Matthew S. Buckland; Siobhan O. Burns; Caterina Cancrini; Pascal Cathébras; Marina Cavazzana; Morgane Cheminant; Matteo Chinello; Peter Ciznar; Tanya I. Coulter; Maud D’Aveni; Olov Ekwall; Zelimir Eric; Efrem Eren; Anders Fasth; Pierre Frange; Benjamin Fournier; Marina Garcia-Prat; Martine Gardembas; Christoph Geier; Sujal Ghosh; Vera Goda; Lennart Hammarström; Fabian Hauck; Maximilian Heeg; Edyta Heropolitanska-Pliszka; Anna Hilfanova; Stephen Jolles; Elif Karakoc-Aydiner; Gerhard R. Kindle; Ayca Kiykim; Christian Klemann; Patra Koletsi; Sylwia Koltan; Irina Kondratenko; Julia Körholz; Renate Krüger; Eric Jeziorski; Romain Levy; Guillaume Le Guenno; Guillaume Lefevre; Vassilios Lougaris; Antonio Marzollo; Nizar Mahlaoui; Marion Malphettes; Andrea Meinhardt; Etienne Merlin; Isabelle Meyts; Tomas Milota; Fernando Moreira; Despina Moshous; Anna Mukhina; Olaf Neth; Jennifer Neubert; Benedicte Neven; Alexandra Nieters; Raphaele Nove-Josserand; Eric Oksenhendler; Ahmet Ozen; Peter Olbrich; Antoinette Perlat; Malgorzata Pac; Jana Pachlopnik Schmid; Lucia Pacillo; Alba Parra-Martinez; Olga Paschenko; Isabelle Pellier; Asena Pinar Sefer; Alessandro Plebani; Dominique Plantaz; Seraina Prader; Loic Raffray; Henrike Ritterbusch; Jacques G. Riviere; Beatrice Rivalta; Stephan Rusch; Inga Sakovich; Sinisa Savic; Raphael Scheible; Nicolas Schleinitz; Catharina Schuetz; Ansgar Schulz; Anna Sediva; Michaela Semeraro; Svetlana O. Sharapova; Anna Shcherbina; Mary A. Slatter; Georgios Sogkas; Pere Soler-Palacin; Carsten Speckmann; Jean-Louis Stephan; Felipe Suarez; Alberto Tommasini; Johannes Trück; Annette Uhlmann; Koen J. van Aerde; Joris van Montfrans; Horst von Bernuth; Klaus Warnatz; Tony Williams; Austen J.J. Worth; Winnie Ip; Capucine Picard; Emilie Catherinot; Zohreh Nademi; Bodo Grimbacher; Lisa R. Forbes Satter; Sven Kracker; Anita Chandra; Alison M. Condliffe; Stephan Ehl; Markus G. Seidel; Mikko R.J. Seppänen; Andrew Gennery; Maria G. Kanariou; Sofia Tantou; Sofia Grigoriadou; Gabriella Cericola; Leif G. Hanitsch; Carmen Scheibenbogen; Eva O. Hlaváčková; Gergely Krivan; Frances K. McGuire; Timothy Ronan Leahy; John David M. Edgar; Shahrzad Bakhtiar; Peter Bader; Geraldine Blanchard Rohner; Filomeen Haerynck; Karlien Claes; Kai Lehmberg; Ingo Müller; Susan Farmand; Maria Fasshauer; Dagmar Graf; Joao Farela Neves; Larysa Kostyuchenko; Luis Ignacio Gonzalez-Granado; Miloš Jeseňák; Maria Carrabba; Giovanna Fabio; Claudio Pignata; Giuliana Giardino; Ilknur Kökçü Karadağ; Alişan Yıldıran; Gonca Hancioglu; Pavlína Králíčková; Sandra Steinmann; Barbara Maria Pietrucha; Michael Gernert; Maarja Soomann; Torsten Witte; Adam Markocsy; Beata Wolska-Kusnierz; Philippe Randrianomenjanahary; Jérémie Rouger; Stavroula Kostaridou; Dariia V. Zabara; Yulia A. Rodina; Oksana A. Shvets

Digital.CSIC. Repositorio Institucional del CSIC
Consejo Superior de Investigaciones Científicas (CSIC)
Journal of Allergy and Clinical Immunology, 152, 4, pp. 984-996.e10

Ginn, SL; Hallwirth, CV; Liao, SHY; Teber, ET; Arthur, JW; Wu, J; Lee, HC; Tay, SS; Hu, M; Reddel, RR; McCormack, MP; Thrasher, AJ; Cavazzana, M; Alexander, SI; Alexander, IE

Mol Ther Nucleic Acids
Molecular Therapy: Nucleic Acids, Vol 6, Iss, Pp 1-14 (2017)

Soheili, T; Rivière, J; Ricciardelli, I; Durand, A; Verhoeyen, E; Derrien, AC; Lagresle-Peyrou, C; de Saint Basile, G; Cosset, FL; Amrolia, P; André-Schmutz, I; Cavazzana, M

Blood. 128:2859-2862

Rubio, Marie-Thérèse; Bouillié, M.; Bouazza, N; Coman, T.; Trebeden-Nègre, H; Gomez, A.; Suarez, Felipe; Sibon, David; Brignier, A; Paubelle, E; Nguyen-Khoc, S; Cavazzana, M; Lantz, O.; Mohty, M.; Urien, S.; Hermine, O.

Leukemia. 31:903-912

Deeks, Sg; Lewin, Sr; Ross, Al; Ananworanich, J; Benkirane, M; Cannon, P; Chomont, N; Douek, D; Lifson, Jd; Lo, Yr; Kuritzkes, D; Margolis, D; Mellors, J; Persaud, D; Tucker, Jd; Barre-Sinoussi, F; International Aids Society Towards a Cure Working Group, International Aids Society Towards a Cure Working Group; Alter, G; Auerbach, J; Autran, B; Barouch, Dh; Behrens, G; Cavazzana, M; Chen, Z; Cohen, Ea; Corbelli, Gm; Eholié, S; Eyal, N; Fidier, S; Garcia, L; Grossman, C; Henderson, G; Henrich, Tj; Jefferys, R; Kiem, Hp; Mccune, J; Moodley, K; Newman, Pa; Nijhuis, M; Nsubuga, Ms; Ott, M; Palmer, S; Richman, D; Saez-Cirion, A; Sharp, M; Siliciano, J; Silvestri, G; Singh, J; Spire, B; Taylor, J; Tolstrup, M; Valente, S; van Lunzen, J; Walensky, R; Wilson, I; Zack, J

Nature Medicine, vol 22, iss 8
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Nature Medicine

Schuetz C; Department of Paediatrics, Universitätsklinikum Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.; Gerke J; Department of Paediatrics, Universitätsklinikum Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.; Ege M; Dr. von Hauner Children's Hospital at Ludwig-Maximilians-Universität, München, Germany.; Helmholtz Zentrum München, Neuherberg, Germany.; Walter J; Division of Allergy and Immunology, Department of Pediatrics, Morsani College of Medicine, University of South Florida, Tampa, FL.; Division of Allergy and Immunology, Department of Medicine, Johns Hopkins All Children's Hospital, St. Petersburg, FL.; Kusters M; Department of Immunology and Gene therapy, Great Ormond Street Hospital, NHS Foundation trust, London, United Kingdom.; Worth A; Department of Immunology and Gene therapy, Great Ormond Street Hospital, NHS Foundation trust, London, United Kingdom.; Kanakry JA; Experimental Transplantation and Immunology Branch, National Cancer Institute, National Institutes of Health, Bethesda, MD.; Dimitrova D; Experimental Transplantation and Immunology Branch, National Cancer Institute, National Institutes of Health, Bethesda, MD.; Wolska-Kuśnierz B; Department of Immunology, Children's Memorial Health Institute, Warsaw, Poland.; Chen K; Division of Allergy and Immunology, Department of Pediatrics, University of Utah School of Medicine, Salt Lake City, UT.; Unal E; Division of Pediatric Hematology and Oncology, Department of Pediatrics, Erciyes University, Kayseri, Turkey.; Karakukcu M; Division of Pediatric Hematology and Oncology, Department of Pediatrics, Erciyes University, Kayseri, Turkey.; Pashchenko O; Department of Immunology, Pirogov Russian National Research Medical University, Moscow, Russia.; Leiding J; Division of Allergy and Immunology, Department of Pediatrics, Johns Hopkins University, Orlando Health Arnold Pamer Hospital for Children, Orlando, FL.; Kawai T; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD.; Amrolia PJ; Bone Marrow Transplant Unit, Great Ormond Street Hospital NHS Foundation Trust, London, United Kingdom.; Berghuis D; Department of Pediatrics, Willem-Alexander Children's Hospital, Leiden University Medical Center, Leiden, The Netherlands.; Buechner J; Department of Pediatric Hematology and Oncology, Oslo University Hospital, Oslo, Norway.; Buchbinder D; Division of Hematology, Children's Hospital of Orange County, Orange, CA.; Cowan MJ; Division of Allergy, Immunology, and Blood and Marrow Transplant, Department of Pediatrics, University of California San Francisco, San Francisco, CA.; Gennery AR; Translational and Clinical Research Institute, Newcastle University, Paediatric Haematopoietic Stem Cell Transplant Unit, Great North Children's Hospital, Newcastle upon Tyne, United Kingdom.; Güngör T; Department of Hematology/Oncology/Immunology, Gene-therapy, and Stem Cell Transplantation, University Children's Hospital Zurich-Eleonore Foundation & Children's Research Center, Zürich, Switzerland.; Heimall J; Division of Allergy and Immunology, Children's Hospital of Philadelphia, Philadelphia, PA.; Department of Pediatrics, Perelman School of Medicine at University of Pennsylvania, Philadelphia, PA.; Miano M; IRCCS Istituto Giannina Gaslini, Genova, Italy.; Meyts I; Department of Pediatrics, Department of Microbiology and Immunology, University Hospitals Leuven, Leuven, Belgium.; Morris EC; UCL Institute of Immunity & Transplantation, University College London Hospitals NHS Foundation Trust, Royal Free London Hospital NHS Foundation Trust, London, United Kingdom.; Rivière J; Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron Research Institute, Hospital Universitari Vall d'Hebron, Universitat Autònoma de Barcelona, Barcelona, Spain.; Sharapova SO; Research Department, Belarusian Research Center for Pediatric Oncology, Hematology and Immunology, Minsk, Belarus.; Shaw PJ; Blood Transplant and Cell Therapies, Children's Hospital at Westmead, Sydney, Australia.; Slatter M; 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Institut Imagine, Paris Descartes-Sorbonne Paris Cité University, Paris, France.; Schulz A; Department of Pediatrics and Adolescent Medicine, Ulm University, Ulm, Germany.; Albert MH; Pediatric SCT Program, Dr. von Hauner University Children's Hospital, Ludwig-Maximilians Universität, München, Germany.; Puck JM; Division of Allergy, Immunology, and Blood and Marrow Transplant, Department of Pediatrics, University of California San Francisco, San Francisco, CA.; Lankester AC; Department of Pediatrics, Willem-Alexander Children's Hospital, Leiden University Medical Center, Leiden, The Netherlands.; Notarangelo LD; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institutes of Health, Bethesda, MD.; Neven B; Paediatric Immunology, Department of Immunology, Haematology and Rheumatology, Necker-Enfants Malades, Paris, France.

Publisher: Elsevier Country of Publication: United States NLM ID: 7603509 Publication Model: Print Cited Medium: Internet ISSN: 1528-0020 (Electronic) Linking ISSN: 00064971 NLM ISO Abbreviation: Blood Subsets: MEDLINE

Poletti, V; Charrier, S; Corre, G; Martin, S; Gjata, B; Vignaud, A; Zhang, F; Buckland, K; Andre-Schmutz, I; Rothe, M; Schambach, A; Pai, S-Y; Williams, DA; Gaspar, HB; Cavazzana, M; Thrasher, AJ; Mavilio, F

Magnani A; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.; Semeraro M; Clinical Investigation Center CIC 1419, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Université de Paris, Assistance Publique-Hôpitaux de Paris, Paris, France.; Adam F; INSERM, UMR_S1176, Université Paris-Saclay, Le Kremlin-Bicêtre, France.; Booth C; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Molecular and Cellular Immunology Section, UCL Great Ormond Street Institute of Child Health, London, UK.; Dupré L; Toulouse Institute for Infectious and Inflammatory Diseases (INFINITy), INSERM, CNRS, Toulouse III Paul Sabatier University, Toulouse, France.; Ludwig Boltzmann Institute for Rare and Undiagnosed Diseases, Vienna, Austria.; Department of Dermatology, Medical University of Vienna, Vienna, Austria.; Morris EC; Institute of Immunity and Transplantation, University College London, London, UK.; Department of Immunology, Royal Free London Hospitals NHS Foundation Trust, London, UK.; Gabrion A; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.; Roudaut C; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.; Borgel D; INSERM, UMR_S1176, Université Paris-Saclay, Le Kremlin-Bicêtre, France.; Laboratoire d'Hématologie, Assistance Publique-Hôpitaux de Paris, Hôpital Necker-Enfants Malades, Paris, France.; Toubert A; EMiLy, INSERM U1160, Institut de Recherche Saint Louis, Université de Paris, Paris, France.; Laboratoire d'Immunologie et d'Histocompatibilité, Hôpital Saint-Louis, Assistance Publique-Hôpitaux de Paris, Paris, France.; Clave E; EMiLy, INSERM U1160, Institut de Recherche Saint Louis, Université de Paris, Paris, France.; Abdo C; Institut Necker-Enfants Malades (INEM), INSERM U1151, Université Paris Descartes Sorbonne Cité, Paris, France.; Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Gorochov G; Département d'Immunologie, Groupement Hospitalier Pitié-Salpêtrière, Assistance Publique-Hôpitaux de Paris, Paris, France.; Centre d'Immunologie et des Maladies Infectieuses-Paris (CIMI-Paris), INSERM, Sorbonne Université, Paris, France.; Petermann R; Platelet Immunology Department, INTS, Paris, France.; Guiot M; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Miyara M; Département d'Immunologie, Groupement Hospitalier Pitié-Salpêtrière, Assistance Publique-Hôpitaux de Paris, Paris, France.; Centre d'Immunologie et des Maladies Infectieuses-Paris (CIMI-Paris), INSERM, Sorbonne Université, Paris, France.; Moshous D; Department of Pediatric Immunology, Hematology and Rheumatology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Imagine Institute, Université Paris Centre, Paris, France.; Magrin E; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.; Denis A; Human Lymphohematopoiesis Laboratory, Imagine Institute, INSERM UMR 1163, Université de Paris, Paris, France.; Suarez F; Imagine Institute, Université Paris Centre, Paris, France.; Service d'Hématologie Adultes, Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris, Centre Université de Paris, Paris, France.; Lagresle C; Human Lymphohematopoiesis Laboratory, Imagine Institute, INSERM UMR 1163, Université de Paris, Paris, France.; Roche AM; Department of Microbiology, University of Pennsylvania School of Medicine, Philadelphia, PA, USA.; Everett J; Department of Microbiology, University of Pennsylvania School of Medicine, Philadelphia, PA, USA.; Trinquand A; Institut Necker-Enfants Malades (INEM), INSERM U1151, Université Paris Descartes Sorbonne Cité, Paris, France.; Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Guisset M; Toulouse Institute for Infectious and Inflammatory Diseases (INFINITy), INSERM, CNRS, Toulouse III Paul Sabatier University, Toulouse, France.; Bayford JX; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Hacein-Bey-Abina S; Unité des Technologies Chimiques et Biologiques pour la Santé, CNRS, INSERM, Université de Paris, Paris, France.; Clinical Immunology Laboratory, Groupe Hospitalier Universitaire Paris-Sud, Hôpital Kremlin-Bicêtre, Assistance Publique-Hôpitaux de Paris, Le Kremlin-Bicêtre, France.; Kauskot A; INSERM, UMR_S1176, Université Paris-Saclay, Le Kremlin-Bicêtre, France.; Elfeky R; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Rivat C; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Abbas S; Généthon, Evry, France.; Gaspar HB; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Macintyre E; Institut Necker-Enfants Malades (INEM), INSERM U1151, Université Paris Descartes Sorbonne Cité, Paris, France.; Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Picard C; Imagine Institute, Université Paris Centre, Paris, France.; Study Center for Primary Immunodeficiencies, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Bushman FD; Department of Microbiology, University of Pennsylvania School of Medicine, Philadelphia, PA, USA.; Galy A; Généthon, Evry, France.; Integrare Research Unit UMRS951, Université Paris-Saclay, Université d'Evry, Inserm, Genethon, Evry, France.; Fischer A; Department of Pediatric Immunology, Hematology and Rheumatology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Imagine Institute, Université Paris Centre, Paris, France.; Collège de France, Paris, France.; Six E; Human Lymphohematopoiesis Laboratory, Imagine Institute, INSERM UMR 1163, Université de Paris, Paris, France.; Thrasher AJ; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK. a.thrasher@ucl.ac.uk.; Molecular and Cellular Immunology Section, UCL Great Ormond Street Institute of Child Health, London, UK. a.thrasher@ucl.ac.uk.; Cavazzana M; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France. m.cavazzana@aphp.fr.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France. m.cavazzana@aphp.fr.; Imagine Institute, Université Paris Centre, Paris, France. m.cavazzana@aphp.fr.

Publisher: Nature Publishing Company Country of Publication: United States NLM ID: 9502015 Publication Model: Print Cited Medium: Internet ISSN: 1546-170X (Electronic) Linking ISSN: 10788956 NLM ISO Abbreviation: Nat Med Subsets: MEDLINE; PubMed not MEDLINE

Maria Elena Maccari; Hassan Abolhassani; Asghar Aghamohammadi; Alessandro Aiuti; Olga Aleinikova; Catherine Bangs; Safa Baris; Federica Barzaghi; Helen Baxendale; Matthew Buckland; Siobhan O. Burns; Caterina Cancrini; Andrew Cant; Pascal Cathébras; Marina Cavazzana; Anita Chandra; Francesca Conti; Tanya Coulter; Lisa A. Devlin; J. David M. Edgar; Saul Faust; Alain Fischer; Marina Garcia Prat; Lennart Hammarström; Maximilian Heeg; Stephen Jolles; Elif Karakoc-Aydiner; Gerhard Kindle; Ayca Kiykim; Dinakantha Kumararatne; Bodo Grimbacher; Hilary Longhurst; Nizar Mahlaoui; Tomas Milota; Fernando Moreira; Despina Moshous; Anna Mukhina; Olaf Neth; Benedicte Neven; Alexandra Nieters; Peter Olbrich; Ahmet Ozen; Jana Pachlopnik Schmid; Capucine Picard; Seraina Prader; William Rae; Janine Reichenbach; Stephan Rusch; Sinisa Savic; Alessia Scarselli; Raphael Scheible; Anna Sediva; Svetlana O. Sharapova; Anna Shcherbina; Mary Slatter; Pere Soler-Palacin; Aurelie Stanislas; Felipe Suarez; Francesca Tucci; Annette Uhlmann; Joris van Montfrans; Klaus Warnatz; Anthony Peter Williams; Phil Wood; Sven Kracker; Alison Mary Condliffe; Stephan Ehl

Front Immunol
RISalud-ANDALUCIA. Repositorio Institucional de Salud de Andalucía
instname
Digital.CSIC. Repositorio Institucional del CSIC
Frontiers in Immunology, Vol 9 (2018)

Magnani A; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.; Semeraro M; Clinical Investigation Center CIC 1419, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Université de Paris, Assistance Publique-Hôpitaux de Paris, Paris, France.; Adam F; INSERM, UMR_S1176, Université Paris-Saclay, Le Kremlin-Bicêtre, France.; Booth C; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Molecular and Cellular Immunology Section, UCL Great Ormond Street Institute of Child Health, London, UK.; Dupré L; Toulouse Institute for Infectious and Inflammatory Diseases (INFINITy), INSERM, CNRS, Toulouse III Paul Sabatier University, Toulouse, France.; Ludwig Boltzmann Institute for Rare and Undiagnosed Diseases, Vienna, Austria.; Department of Dermatology, Medical University of Vienna, Vienna, Austria.; Morris EC; Institute of Immunity and Transplantation, University College London, London, UK.; Department of Immunology, Royal Free London Hospitals NHS Foundation Trust, London, UK.; Gabrion A; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.; Roudaut C; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.; Borgel D; INSERM, UMR_S1176, Université Paris-Saclay, Le Kremlin-Bicêtre, France.; Laboratoire d'Hématologie, Assistance Publique-Hôpitaux de Paris, Hôpital Necker-Enfants Malades, Paris, France.; Toubert A; EMiLy, INSERM U1160, Institut de Recherche Saint Louis, Université de Paris, Paris, France.; Laboratoire d'Immunologie et d'Histocompatibilité, Hôpital Saint-Louis, Assistance Publique-Hôpitaux de Paris, Paris, France.; Clave E; EMiLy, INSERM U1160, Institut de Recherche Saint Louis, Université de Paris, Paris, France.; Abdo C; Institut Necker-Enfants Malades (INEM), INSERM U1151, Université Paris Descartes Sorbonne Cité, Paris, France.; Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Gorochov G; Département d'Immunologie, Groupement Hospitalier Pitié-Salpêtrière, Assistance Publique-Hôpitaux de Paris, Paris, France.; Centre d'Immunologie et des Maladies Infectieuses-Paris (CIMI-Paris), INSERM, Sorbonne Université, Paris, France.; Petermann R; Platelet Immunology Department, INTS, Paris, France.; Guiot M; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Miyara M; Département d'Immunologie, Groupement Hospitalier Pitié-Salpêtrière, Assistance Publique-Hôpitaux de Paris, Paris, France.; Centre d'Immunologie et des Maladies Infectieuses-Paris (CIMI-Paris), INSERM, Sorbonne Université, Paris, France.; Moshous D; Department of Pediatric Immunology, Hematology and Rheumatology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Imagine Institute, Université Paris Centre, Paris, France.; Magrin E; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.; Denis A; Human Lymphohematopoiesis Laboratory, Imagine Institute, INSERM UMR 1163, Université de Paris, Paris, France.; Suarez F; Imagine Institute, Université Paris Centre, Paris, France.; Service d'Hématologie Adultes, Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris, Centre Université de Paris, Paris, France.; Lagresle C; Human Lymphohematopoiesis Laboratory, Imagine Institute, INSERM UMR 1163, Université de Paris, Paris, France.; Roche AM; Department of Microbiology, University of Pennsylvania School of Medicine, Philadelphia, PA, USA.; Everett J; Department of Microbiology, University of Pennsylvania School of Medicine, Philadelphia, PA, USA.; Trinquand A; Institut Necker-Enfants Malades (INEM), INSERM U1151, Université Paris Descartes Sorbonne Cité, Paris, France.; Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Guisset M; Toulouse Institute for Infectious and Inflammatory Diseases (INFINITy), INSERM, CNRS, Toulouse III Paul Sabatier University, Toulouse, France.; Bayford JX; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Hacein-Bey-Abina S; Unité des Technologies Chimiques et Biologiques pour la Santé, CNRS, INSERM, Université de Paris, Paris, France.; Clinical Immunology Laboratory, Groupe Hospitalier Universitaire Paris-Sud, Hôpital Kremlin-Bicêtre, Assistance Publique-Hôpitaux de Paris, Le Kremlin-Bicêtre, France.; Kauskot A; INSERM, UMR_S1176, Université Paris-Saclay, Le Kremlin-Bicêtre, France.; Elfeky R; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Rivat C; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Abbas S; Généthon, Evry, France.; Gaspar HB; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.; Macintyre E; Institut Necker-Enfants Malades (INEM), INSERM U1151, Université Paris Descartes Sorbonne Cité, Paris, France.; Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Picard C; Imagine Institute, Université Paris Centre, Paris, France.; Study Center for Primary Immunodeficiencies, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Bushman FD; Department of Microbiology, University of Pennsylvania School of Medicine, Philadelphia, PA, USA.; Galy A; Généthon, Evry, France.; Integrare Research Unit UMRS951, Université Paris-Saclay, Université d'Evry, Inserm, Genethon, Evry, France.; Fischer A; Department of Pediatric Immunology, Hematology and Rheumatology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.; Imagine Institute, Université Paris Centre, Paris, France.; Collège de France, Paris, France.; Six E; Human Lymphohematopoiesis Laboratory, Imagine Institute, INSERM UMR 1163, Université de Paris, Paris, France.; Thrasher AJ; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK. a.thrasher@ucl.ac.uk.; Molecular and Cellular Immunology Section, UCL Great Ormond Street Institute of Child Health, London, UK. a.thrasher@ucl.ac.uk.; Cavazzana M; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France. m.cavazzana@aphp.fr.; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France. m.cavazzana@aphp.fr.; Imagine Institute, Université Paris Centre, Paris, France. m.cavazzana@aphp.fr.

Publisher: Nature Publishing Company Country of Publication: United States NLM ID: 9502015 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1546-170X (Electronic) Linking ISSN: 10788956 NLM ISO Abbreviation: Nat Med Subsets: MEDLINE

Poletti, V; Charrier, S; Urbinati, F; Hollis, RP; Corre, G; Martin, S; Weber, L; Rothe, M; Schambach, A; Miccio, A; Cavazzana, M; Kohn, DB; Mavilio, F

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