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In: Blood Advances . (Blood Advances, 9 April 2024, 8(7):1796-1803)
Academic Journal
Elkouby, L.; Davidson, R.J.; Nguyen, G.N.; Sabatino, D.E.; Armour, S.M.; Toso, R.; DiPietro, M.; Willet, M.; Kutza, S.; Silverberg, J.; Frick, J.; Crosariol, M.; Wang, Y.; Wang, C.; High, K.A.; Anguela, X.M.
In: Molecular Therapy Methods and Clinical Development . (Molecular Therapy Methods and Clinical Development, 10 March 2022, 24:20-29)
Academic Journal
Costa-Verdera, H.; Collaud, F.; Sellier, P.; Cagin, U.; Fabregue, J.; Barral, S.; van Wittenberghe, L.; Daniele, N.; Gjata, B.; Cosette, J.; Simon-Sola, M.; Charles, S.; Gross, D.A.; Colella, P.; Ronzitti, G.; Mingozzi, F.; Riling, C.R.; Nordin, J.M.L.; Preston, G.M.; Li, M.; Crosariol, M.; Antrilli, T.; Quinn, W.J.; Anguela, X.M.; Armour, S.M.; Moya-Nilges, M.; Krijnse-Locker, J.; Abad, C.; Boyer, O.
In: Nature Communications . (Nature Communications, December 2021, 12(1))
Academic Journal
George, L.A.; Samelson-Jones, B.J.; Monahan, P.E.; MacDougall, A.; Jaworski, K.; Noble, R.; Curran, M.; Kuranda, K.; Mingozzi, F.; Chang, T.; Reape, K.Z.; Anguela, X.M.; High, K.A.; Elaine Eyster, M.; Ragni, M.V.; Sullivan, S.K.; Croteau, S.E.; Rasko, J.E.J.; Recht, M.
In: New England Journal of Medicine . (New England Journal of Medicine, 18 November 2021, 385(21):1961-1973)
Academic Journal
Zou, C.; de Jong, Y.P.; Vercauteren, K.O.A.; Michailidis, E.; Kabbani, M.; Quirk, C.; Meuleman, P.; Zoluthkin, I.; Chiriboga, L.; Yazicioglu, M.; Anguela, X.M.; High, K.A.; Herzog, R.W.
In: Molecular Therapy Methods and Clinical Development . (Molecular Therapy Methods and Clinical Development, 11 September 2020, 18:189-198)
Academic Journal
George, L.A.; Raffini, L.J.; Samelson-Jones, B.J.; High, K.A.; Runowski, A.R.; Ragni, M.V.; Rasko, J.E.J.; Ozelo, M.; Hazbon, M.; Wellman, J.A.; Wachtel, K.; Chen, Y.; Anguela, X.M.; Kuranda, K.; Mingozzi, F.
In: Molecular Therapy . (Molecular Therapy, 2 September 2020, 28(9):2073-2082)
Academic Journal
Leborgne, C.; Barbon, E.; Collaud, F.; van Wittengerghe, L.; Marolleau, B.; Miranda, A.; Fabiano, A.; Ronzitti, G.; Mingozzi, F.; Alexander, J.M.; Hanby, H.; Cohen, D.M.; Muraleetharan, S.; Lupo, D.; Silverberg, J.; Huang, K.; Beck, H.; Anguela, X.M.; Armour, S.M.; Delignat, S.; Daventure, V.; Lacroix-Desmazes, S.
In: Nature Medicine . (Nature Medicine, 1 July 2020, 26(7):1096-1101)
Academic Journal
George, L.A.; Samelson-Jones, B.J.; Winters, A.; Arruda, V.R.; Van Der Loo, J.C.M.; Zelenaia, O.; Cuker, A.; Luk, A.Y.; Hui, D.; Wright, J.F.; Chen, Y.; Liu, Y.; Wachtel, K.; Takefman, D.; Carr, M.E.; Couto, L.B.; Anguela, X.M.; High, K.A.; Sullivan, S.K.; Sullivan, L.M.; Majumdar, S.; Giermasz, A.; Ducore, J.; Rasko, J.E.J.; Teitel, J.; McGuinn, C.E.; Ragni, M.V.; Tiefenbacher, S.
In: New England Journal of Medicine . (New England Journal of Medicine, 7 December 2017, 377(23):2215-2227)
Academic Journal
In: Human Molecular Genetics . (Human Molecular Genetics, 15 April 2016, 25(R1):R36-R41)
Academic Journal
Sharma, R.; Anguela, X.M.; Davidson, R.J.; Zhou, S.; Rieders, J.; High, K.A.; Doyon, Y.; Wechsler, T.; DeKelver, R.C.; Sproul, S.; Paschon, D.E.; Miller, J.C.; Shivak, D.; Gregory, P.D.; Holmes, M.C.; Rebar, E.J.
In: Blood . (Blood, 8 October 2015, 126(15):1777-1784)
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[AR] Anguela, X.M.
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