e-Article
Comparative Studies Reveal Robust HbF Induction By Editing of HBG1/2 Promoters or BCL11A Erythroid-Enhancer in Human CD34+Cells but That BCL11A Erythroid-Enhancer Editing Is Associated with Selective Reduction in Erythroid Lineage Reconstitution in a Xenotransplantation Model
Document Type
Journal
Author
Chang, Kai-Hsin; Sanchez, Minerva; Heath, Jack; dedreuzy, Edouard; Haskett, Scott; Vogelaar, Abigail; Gogi, Kiran; Da Silva, Jen; Wang, Tongyao; Sadowski, Andrew; Gotta, Gregory; Siwak, Jamaica; Viswanathan, Ramya; Loveluck, Katherine; Chao, Hoson; Tillotson, Eric; Chalishazar, Aditi; Dass, Abhishek; Ta, Frederick; Brennan, Emily; Tabbaa, Diana; Marco, Eugenio; Zuris, John A.; Reyon, Deepak; Isik, Meltem; Friedland, Ari; Ta, Terence; Harbinski, Fred; Giannoukos, Georgia; Teixeira, Sandra; Wilson, Christopher J.; Albright, Charlie; Jiang, Haiyan
Source
Subject
Language
English
ISSN
15280020