e-Article
Correction of a urea cycle defect after ex vivo gene editing of human hepatocytes
Document Type
Article
Author
Zabulica, M.; Srinivasan, R.C.; Hammarstedt, C.; Jakobsson, T.; Gramignoli, R.; Strom, S.C.; Akcakaya, P.; Bestas, B.; Forslöw, A.; Engberg, S.; Maresca, M.; Allegri, G.; Makris, G.; Scherer, T.; Rimann, N.; Thöny, B.; Häberle, J.; Firth, M.; Rosen, B.; Jakobsson, T.; Ellis, E.; Jorns, C.; Rooyackers, O.; van Zuydam, N.R.
Source
In: Molecular Therapy . (Molecular Therapy, 5 May 2021, 29(5):1903-1917)
Subject
Language
English
ISSN
15250024
15250016
15250016