학술논문
'학술논문'
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Academic Journal
Grunseich, Christopher; Miller, Ram; Swan, Therese; Glass, David J; Mouelhi, Mohamed El; Fornaro, Mara; Petricoul, Olivier; Vostiar, Igor; Roubenoff, Ronenn; Meriggioli, Matthew N; Kokkinis, Angela; Guber, Robert D; Budron, Maher S; Vissing, John; Soraru, Gianni; Mozaffar, Tahseen; Ludolph, Albert; Kissel, John T; Fischbeck, Kenneth H; group, BVS857 study; Dahlqvist, Julia; Witting, Nanna; Martinelli, Ilaria; Querin, Giorgia; Goyal, Namita A; Cash, Tiyonnoh M; Minton, Brian; Rosenbohm, Angela; Weiland, Ulrike; Weydt, Patrick; Chelnick, Sharon; Iyadurai, Stanley; King, Wendy
The Lancet Neurology. 17(12)
Academic Journal
Burns, Ted M.; Smith, Gordon A.; Allen, Jeffrey A.; Amato, Anthony A.; Arnold, David W.; Barohn, Richard; Benatar, Michael; Bird, Shawn J.; Bromberg, Mark; Chahin, Nizar; Ciafaloni, Emma; Cohen, Jeffrey A.; Corse, Andrea; Crum, Brian A.; David, William S.; Dimberg, Elliot; Sousa, Eduardo A. De; Donofrio, Peter D.; Dyck, James P. B.; Engel, Andrew G.; Ensrud, Erik R.; Ferrante, Mark; Freimer, Miriam; Gable, Karissa L.; Gibson, Summer; Gilchrist, James M.; Goldstein, Jonathan M.; Gooch, Clifton L.; Goodman, Brent P.; Gorelov, Dmitri; Gospe, Sidney M., Jr.; Goyal, Namita A.; Guidon, Amanda C.; Guptill, Jeffrey T.; Gutmann, Laurie; Gutmann, Ludwig; Gwathmey, Kelly; Harati, Yadollah; Harper, Michel C., Jr.; Hehir, Michael K.; Hobson-Webb, Lisa D.; Howard, James F., Jr.; Jackson, Carlayne E.; Johnson, Nicholas; Jones, Sarah M.; Juel, Vern C.; Kaminski, Henry J.; Karam, Chafic; Kennelly, Kathleen D.; Khella, Sami; Khoury, Julie; Kincaid, John C.; Kissel, John T.; Kolb, Noah; Lacomis, David; Ladha, Shafeeq; Larriviere, Daniel; Lewis, Richard A.; Li, Yuebing; Litchy, William J.; Logigian, Eric; Lou, Jau-Shin; MacGowen, Daniel J.L.; Maselli, Ricardo; Massey, Janice M.; Mauermann, Michelle L.; Mathews, Katherine D.; Meriggioli, Matthew N.; Miller, Robert G.; Moon, Joon-Shik; Mozaffar, Tahseen; Nations, Sharon P.; Nowak, Richard J.; Ostrow, Lyle W.; Pascuzzi, Robert M.; Peltier, Amanda; Ruzhansky, Katherine; Richman, David P.; Ross, Mark A.; Rubin, DEVON I.; Russell, James A.; Sachs, George M.; Salajegheh, Mohammad Kian; Saperstein, David S.; Scelsa, Stephen; Selcen, Duygu; Shaibani, Aziz; Shieh, Perry B.; Silvestri, Nicholas J.; Singleton, Rob J.; Smith, Benn E.; So, Yuen T.; Solorzano, Guillermo; Sorenson, Eric J.; Srinivasen, Jayashri; Tavee, Jinny; Tawil, Rabi; Thaisetthawatkul, Pariwat; Thornton, Charles; Trivedi, Jaya; Vernino, Steven; Wang, Annabel K.; Webb, Tyler A.; Weiss, Michael D.; Windebank, Anthony J.; Wolfe, Gil I.
Muscle & Nerve. Feb 01, 2016 53(2):165-168
Academic Journal
BENATAR, MICHAEL; SANDERS, DONALD B.; BURNS, TED M.; CUTTER, GARY R.; GUPTILL, JEFFREY T.; BAGGI, FULVIO; KAMINSKI, HENRY J.; MANTEGAZZA, RENATO; MERIGGIOLI, MATTHEW N.; QUAN, JOANNE; WOLFE, GIL I.
Muscle & Nerve. Jun 01, 2012 45(6):909-917
Academic Journal
Benatar M; Sanders DB; Burns TM; Cutter GR; Guptill JT; Baggi F; Kaminski HJ; Mantegazza R; Meriggioli MN; Quan J; Wolfe GI; 李海峰; 高翔
中国神经免疫学和神经病学杂志 / Chinese Journal of Neuroimmunology and Neurology. 20(1):74-74
Academic Journal
Mendell, J.; Finkel, R.; Mercuri, E.; Strauss, K.; Day, J.; Kleyn, A.; Chand, D.; Tauscher-Wisniewski, S.; Meriggioli, M.
In Neuromuscular Disorders October 2021 31 Supplement 1:S132-S133
Academic Journal
Amato, A.A.; Hanna, M.G.; Machado, P.M.; Badrising, U.A.; Chinoy, H.; Benveniste, O.; Karanam, A.K.; Wu, M.; Papanicolaou, D.A.; Tankó, L.B.; Schubert-Tennigkeit, A.A.; Lloyd, T.E.; Needham, M.; Liang, C.; Reardon, K.A.; de Visser, M.; Ascherman, D.P.; Barohn, R.J.; Dimachkie, M.M.; Miller, J.A.L.; Kissel, J.T.; Oskarsson, B.; Joyce, N.C.; Van den Bergh, P.; Baets, J.; De Bleecker, J.L.; Karam, C.; David, W.S.; Mirabella, M.; Nations, S.P.; Jung, H.H.; Pegoraro, E.; Maggi, L.; Rodolico, C.; Filosto, M.; Shaibani, A.I.; Sivakumar, K.; Goyal, N.A.; Mori-Yoshimura, M.; Yamashita, S.; Suzuki, N.; Aoki, M.; Katsuno, M.; Morihata, H.; Murata, K.; Nodera, H.; Nishino, I.; Romano, C.D.; Williams, V.S.L.; Vissing, J.; Auberson, L.Z.; Everett, B.; Pradhan, A.D.; Taqueti, V.; Olenchock, B.; Blauth, M.; Kammerlander, C.; Krappinger, D.; Colon-Emeric, C.; Velazquez, E.; Meriggioli, M.; Huhtaniemi, I.; Magaziner, J.; Evans, S.R.; Griggs, R.
In: Neurology . (Neurology, 2021, 96(12):E1595-E1607)
Academic Journal
In Value in Health November 2019 22 Supplement 3:S739-S739
Academic Journal
Finkel, R.S.; Day, J.W.; Darras, B.T.; Kuntz, N.L.; Connolly, A.M.; Crawford, T.O.; Butterfield, R.J.; Shieh, P.B.; Tennekoon, G.; Iannaccone, S.T.; Meriggioli, M.; Ogrinc, F.G.; Kavanagh, S.; Kernbauer, E.; Whittle, J.; L'Italien, J.; Kaspar, B.; Sproule, D.M.; Spector, S.A.; Feltner, D.E.; Mendell, J.R.
In Journal of the Neurological Sciences 15 October 2019 405 Supplement:57-57
Long-term follow-up (LTFU) of onasemnogene abeparvovec gene therapy in spinal muscular atrophy (SMA)
Academic Journal
Mendell, J.; Finkel, R.; Mercuri, E.; Strauss, K.; Day, J.; Kleyn, A.; Chand, D.; Tauscher-Wisniewski, S.; Meriggioli, M.
Long-term Follow-up (LTFU) of Onasemnogene Abeparvovec Gene Therapy in Spinal Muscular Atrophy (SMA)
Academic Journal
Day, J.; Mendell, J.; Finkel, R.; Mercuri, E.; Strauss, K.; Kleyn, A.; Chand, D.; Tauscher-Wisniewski, S.; Meriggioli, M.
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