부산대학교 도서관

Grošelj U; Department of Endocrinology, Diabetes, and Metabolic Diseases, University Children's Hospital, University Medical Centre Ljubljana, Bohoriceva 20, Ljubljana, 1000, Slovenia. urh.groselj@kclj.si.; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia. urh.groselj@kclj.si.; Department of Medical Ethics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia. urh.groselj@kclj.si.; Kavčič M; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Department of Paediatric Haematology and Oncology, University Children's Hospital, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Drole Torkar A; Department of Endocrinology, Diabetes, and Metabolic Diseases, University Children's Hospital, University Medical Centre Ljubljana, Bohoriceva 20, Ljubljana, 1000, Slovenia.; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Kafol J; Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Centre for the Technologies of Gene and Cell Therapy (CTGCT), National Institute of Chemistry, Ljubljana, Slovenia.; Jerala R; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Centre for the Technologies of Gene and Cell Therapy (CTGCT), National Institute of Chemistry, Ljubljana, Slovenia.; Sever M; Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Department of Haematology, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Zver S; Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Department of Haematology, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Serša G; Institute of Oncology Ljubljana, Ljubljana, Slovenia.; Čemažar M; Institute of Oncology Ljubljana, Ljubljana, Slovenia.; Strojan P; Institute of Oncology Ljubljana, Ljubljana, Slovenia.; Grošelj A; Department of Otorhinolaryngology and Cervicofacial Surgery, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Žerjav Tanšek M; Department of Endocrinology, Diabetes, and Metabolic Diseases, University Children's Hospital, University Medical Centre Ljubljana, Bohoriceva 20, Ljubljana, 1000, Slovenia.; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Miroševič Š; Department of Family Medicine, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Ivančan S; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Department of Paediatric Haematology and Oncology, University Children's Hospital, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Prelog T; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Department of Paediatric Haematology and Oncology, University Children's Hospital, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Gosar D; Department of Paediatric Neurology, University Children's Hospital, University Medical Centre Ljubljana, Bohoriceva 20, Ljubljana, 1000, Slovenia.; Oražem Mrak J; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Department of Paediatric Neurology, University Children's Hospital, University Medical Centre Ljubljana, Bohoriceva 20, Ljubljana, 1000, Slovenia.; Mlinarič M; Department of Endocrinology, Diabetes, and Metabolic Diseases, University Children's Hospital, University Medical Centre Ljubljana, Bohoriceva 20, Ljubljana, 1000, Slovenia.; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Bertok S; Department of Endocrinology, Diabetes, and Metabolic Diseases, University Children's Hospital, University Medical Centre Ljubljana, Bohoriceva 20, Ljubljana, 1000, Slovenia.; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Kovač J; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Clinical Institute of Special Laboratory Diagnostics, University Children's Hospital, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Kodrič J; Child Psychiatry Unit, University Children's Hospital, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Battelino S; Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Department of Otorhinolaryngology and Cervicofacial Surgery, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Pokorn M; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; University Children's Hospital, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Department of Infectious Diseases, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Ihan A; Institute of Microbiology and Immunology, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Jazbec J; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Department of Paediatric Haematology and Oncology, University Children's Hospital, University Medical Centre Ljubljana, Ljubljana, Slovenia.; Battelino T; Department of Endocrinology, Diabetes, and Metabolic Diseases, University Children's Hospital, University Medical Centre Ljubljana, Bohoriceva 20, Ljubljana, 1000, Slovenia.; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Osredkar D; Department of Paediatrics, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia. damjan.osredkar@kclj.si.; Department of Paediatric Neurology, University Children's Hospital, University Medical Centre Ljubljana, Bohoriceva 20, Ljubljana, 1000, Slovenia. damjan.osredkar@kclj.si.

Publisher: BioMed Central Country of Publication: England NLM ID: 101266602 Publication Model: Electronic Cited Medium: Internet ISSN: 1750-1172 (Electronic) Linking ISSN: 17501172 NLM ISO Abbreviation: Orphanet J Rare Dis Subsets: MEDLINE

Miroševič Š; CTNNB1 Foundation, The Gene Therapy Research Institute, Dalmatinova ulica 5, Ljubljana 1000, Slovenia.; Department for Family Medicine, Faculty of Medicine, University of Ljubljana, Poljanski nasip 58, Ljubljana 1000, Slovenia.; Khandelwal S; CTNNB1 Foundation, The Gene Therapy Research Institute, Ljubljana, Slovenia.; Amerson E; CTNNB1 Connect & Cure, Green Village, DE, USA.; Parks E; CTNNB1 Connect & Cure, Green Village, DE, USA.; Parks M; CTNNB1 Connect & Cure, Green Village, DE, USA.; Cochran L; CTNNB1 Connect & Cure, Green Village, DE, USA.; González Hernández A; CTNNB1 Foundation, The Gene Therapy Research Institute, Ljubljana, Slovenia.; Asociación CTNNB1 España, Basauri, Spain.; Ferraro M; CTNNB1 Italia, Via Giovanni Leone, ACRI CS, Italy.; Lisowski L; Gene Therapy Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, University of Sydney, Westmead, NSW, Australia.; Perez-Iturralde A; Gene Therapy Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, University of Sydney, Westmead, NSW, Australia.; Chung W; Department of Pediatrics, Boston Children's Hospital, Harvard Medical School, Boston, MA, USA.; Jacob MH; School of Medicine, Tufts University, Boston, MA, USA.; Žakelj N; Department of Pediatric Neurology, University Children's Hospital, Ljubljana, Slovenia.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Center for the Technologies of Gene and Cell Therapy, Ljubljana, Slovenia.; Forstnerič V; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Sušjan P; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Maruna M; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Jerala R; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Osredkar D; Department of Pediatric Neurology, University Children's Hospital, University Medical Centre Ljubljana, Ljubljana, Slovenia.

Publisher: Sage Country of Publication: England NLM ID: 9918557474706676 Publication Model: eCollection Cited Medium: Internet ISSN: 2633-0040 (Electronic) Linking ISSN: 26330040 NLM ISO Abbreviation: Ther Adv Rare Dis Subsets: PubMed not MEDLINE

Orehek S; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Interdisciplinary Doctoral Study of Biomedicine, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Ramuta TŽ; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; EN-FIST Centre of Excellence, Ljubljana, Slovenia.; Centre for the Technologies of Gene and Cell Therapy, National Institute of Chemistry, Ljubljana, Slovenia.; Malenšek Š; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Interdisciplinary Doctoral Study of Biomedicine, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Šala M; Department of Analytical Chemistry, National Institute of Chemistry, Ljubljana, Slovenia.; Benčina M; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; Centre for the Technologies of Gene and Cell Therapy, National Institute of Chemistry, Ljubljana, Slovenia.; Biotechnical Faculty, University of Ljubljana, Ljubljana, Slovenia.; Jerala R; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia.; EN-FIST Centre of Excellence, Ljubljana, Slovenia.; Centre for the Technologies of Gene and Cell Therapy, National Institute of Chemistry, Ljubljana, Slovenia.; Hafner-Bratkovič I; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, Slovenia. iva.hafner@ki.si.; EN-FIST Centre of Excellence, Ljubljana, Slovenia. iva.hafner@ki.si.; Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia. iva.hafner@ki.si.

Publisher: Nature Pub. Group Country of Publication: England NLM ID: 101528555 Publication Model: Electronic Cited Medium: Internet ISSN: 2041-1723 (Electronic) Linking ISSN: 20411723 NLM ISO Abbreviation: Nat Commun Subsets: MEDLINE

Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, 1000, Slovenia. dusko.lainscek@ki.si.; Centre for Technologies of Gene and Cell Therapy, Ljubljana, 1000, Slovenia. dusko.lainscek@ki.si.; EN-FIST Centre of Excellence, Ljubljana, 1000, Slovenia. dusko.lainscek@ki.si.; Forstnerič V; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Ljubljana, 1000, Slovenia. vida.forstneric@ki.si.; Miroševič Š; The Gene Therapy Research Institute, CTNNB1 Foundation, Ljubljana, 1000, Slovenia. spela@ctnnb1-foundation.org.; Department of Family Medicine, Faculty of Medicine Ljubljana, University of Ljubljana, Ljubljana, 1000, Slovenia. spela@ctnnb1-foundation.org.

Publisher: Springer-Verlag Country of Publication: United States NLM ID: 9100916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1432-1777 (Electronic) Linking ISSN: 09388990 NLM ISO Abbreviation: Mamm Genome Subsets: MEDLINE

Žakelj N; Department of Pediatric Neurology, University Children's Hospital, University Medical Centre Ljubljana, Bohoričeva 20, 1525 Ljubljana, Slovenia.; Gosar D; Department of Pediatric Neurology, University Children's Hospital, University Medical Centre Ljubljana, Bohoričeva 20, 1525 Ljubljana, Slovenia.; Miroševič Š; Department of Family Medicine, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia.; Sanders SJ; Institute of Developmental and Regenerative Medicine, Department of Paediatrics, University of Oxford, OX3 7TY Oxford, UK; Department of Psychiatry and Behavioral Sciences, UCSF Weill Institute for Neurosciences, University of California, San Francisco, San Francisco, CA 94158, USA; New York Genome Center, New York, NY 10013, USA.; Ljungdahl A; Institute of Developmental and Regenerative Medicine, Department of Paediatrics, University of Oxford, OX3 7TY Oxford, UK; Department of Psychiatry and Behavioral Sciences, UCSF Weill Institute for Neurosciences, University of California, San Francisco, San Francisco, CA 94158, USA.; Kohani S; Institute of Developmental and Regenerative Medicine, Department of Paediatrics, University of Oxford, OX3 7TY Oxford, UK.; Huang S; School of Life Sciences, Faculty of Science, The Chinese University of Hong Kong, Hong Kong SAR, China.; Leong LI; School of Life Sciences, Faculty of Science, The Chinese University of Hong Kong, Hong Kong SAR, China.; An Y; School of Life Sciences, Faculty of Science, The Chinese University of Hong Kong, Hong Kong SAR, China.; Teo MJ; School of Life Sciences, Faculty of Science, The Chinese University of Hong Kong, Hong Kong SAR, China.; Moultrie F; MDUK Oxford Neuromuscular Centre, Department of Paediatrics, University of Oxford and NIHR Oxford Biomedical Research Center, OX3 9DU Oxford, UK.; Jerala R; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia; Centre for Technologies of Gene and Cell Therapy, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia; Centre for Technologies of Gene and Cell Therapy, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Forstnerič V; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Sušjan P; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Lisowski L; Translational Vectorology Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, The University of Sydney, Westmead, NSW 2145, Australia; Australian Genome Therapeutics Centre, Children's Medical Research Institute and Sydney Children's Hospitals Network, Westmead, NSW 2145, Australia; Laboratory of Molecular Oncology and Innovative Therapies, Military Institute of Medicine - National Research Institute, Warsaw, Poland.; Perez-Iturralde A; Translational Vectorology Research Unit, Children's Medical Research Institute, Faculty of Medicine and Health, The University of Sydney, Westmead, NSW 2145, Australia.; Mrak JO; Department of Pediatric Neurology, University Children's Hospital, University Medical Centre Ljubljana, Bohoričeva 20, 1525 Ljubljana, Slovenia.; Chan HYE; School of Life Sciences, Faculty of Science, The Chinese University of Hong Kong, Hong Kong SAR, China; Gerald Choa Neuroscience Institute, The Chinese University of Hong Kong, Hong Kong SAR, China.; Osredkar D; Department of Pediatric Neurology, University Children's Hospital, University Medical Centre Ljubljana, Bohoričeva 20, 1525 Ljubljana, Slovenia; Center for Developmental Neuroscience, Faculty of Medicine, University of Ljubljana, Ljubljana, Slovenia. Electronic address: damjan.osredkar@kclj.si.

Publisher: Elsevier Inc Country of Publication: United States NLM ID: 101772885 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2666-2477 (Electronic) Linking ISSN: 26662477 NLM ISO Abbreviation: HGG Adv Subsets: MEDLINE

Ivanovski F; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, Ljubljana, Slovenia.; Interfaculty Doctoral Study of Biomedicine, University of Ljubljana, Vrazov trg 2, Ljubljana, Slovenia.; Meško M; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, Ljubljana, Slovenia.; Lebar T; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, Ljubljana, Slovenia.; Rupnik M; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, Ljubljana, Slovenia.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, Ljubljana, Slovenia.; Gradišek M; Faculty of Electrical Engineering, University of Ljubljana, Tržaška c. 25, Ljubljana, Slovenia.; Jerala R; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, Ljubljana, Slovenia. roman.jerala@ki.si.; CTGCT, Centre of Technology of Gene and Cell Therapy, Hajdrihova 19, Ljubljana, Slovenia. roman.jerala@ki.si.; Benčina M; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, Ljubljana, Slovenia. mojca.bencina@ki.si.; CTGCT, Centre of Technology of Gene and Cell Therapy, Hajdrihova 19, Ljubljana, Slovenia. mojca.bencina@ki.si.; University of Ljubljana, Kongresni trg 12, 1000, Ljubljana, Slovenia. mojca.bencina@ki.si.

Publisher: Nature Pub. Group Country of Publication: England NLM ID: 101528555 Publication Model: Electronic Cited Medium: Internet ISSN: 2041-1723 (Electronic) Linking ISSN: 20411723 NLM ISO Abbreviation: Nat Commun Subsets: MEDLINE

Malenšek Š; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Interdisciplinary Doctoral Study of Biomedicine, Medical Faculty, University of Ljubljana, 1000 Ljubljana, Slovenia.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Centre for Technologies of Gene and Cell Therapy, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Esih H; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Interdisciplinary Doctoral Study of Biomedicine, Medical Faculty, University of Ljubljana, 1000 Ljubljana, Slovenia.; Orehek S; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Interdisciplinary Doctoral Study of Biomedicine, Medical Faculty, University of Ljubljana, 1000 Ljubljana, Slovenia.; Fink T; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Urbanc AG; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Blinc A; Department of Vascular Diseases, University Medical Center Ljubljana, 1000 Ljubljana, Slovenia.; Faculty of Medicine, Department of Internal Medicine, University of Ljubljana, 1000 Ljubljana, Slovenia.; Jerala R; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Centre for Technologies of Gene and Cell Therapy, National Institute of Chemistry, 1000 Ljubljana, Slovenia.

Publisher: Cell Press Country of Publication: United States NLM ID: 101624857 Publication Model: eCollection Cited Medium: Print ISSN: 2329-0501 (Print) Linking ISSN: 23290501 NLM ISO Abbreviation: Mol Ther Methods Clin Dev Subsets: PubMed not MEDLINE

Mlakar T; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Interdisciplinary Doctoral Study of Biomedicine, Medical Faculty, University of Ljubljana, 1000 Ljubljana, Slovenia.; Skrbinek M; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Interdisciplinary Doctoral Study of Biomedicine, Medical Faculty, University of Ljubljana, 1000 Ljubljana, Slovenia.; Fink T; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Centre for Technologies of Gene and Cell Therapy, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; Centre for Technologies of Gene and Cell Therapy, National Institute of Chemistry, 1000 Ljubljana, Slovenia.; EN-FIST Centre of Excellence, 1000 Ljubljana, Slovenia.

Publisher: MDPI Country of Publication: Switzerland NLM ID: 101092791 Publication Model: Electronic Cited Medium: Internet ISSN: 1422-0067 (Electronic) Linking ISSN: 14220067 NLM ISO Abbreviation: Int J Mol Sci Subsets: MEDLINE

Cavazza, A.; Hendel, A.; Bak, R.O.; Rio, P.; Güell, M.; Lainšček, D.; Arechavala-Gomeza, V.; Peng, L.; Hapil, F.Z.; Harvey, J.; Ortega, F.G.; Gonzalez-Martinez, C.; Lederer, C.W.; Mikkelsen, K.; Gasiunas, G.; Kalter, N.; Gonçalves, M.A.F.V.; Petersen, J.; Garanto, A.; Montoliu, L.; Maresca, M.; Seemann, S.E.; Gorodkin, J.; Mazini, L.; Sanchez, R.; Rodriguez-Madoz, J.R.; Maldonado-Pérez, N.; Laura, T.; Schmueck-Henneresse, M.; Maccalli, C.; Grünewald, J.; Carmona, G.; Kachamakova-Trojanowska, N.; Miccio, A.; Martin, F.; Turchiano, G.; Cathomen, T.; Luo, Y; Tsai, S.Q.; Benabdellah, K.

Mol Ther Nucleic Acids
Digibug. Repositorio Institucional de la Universidad de Granada
Universidad de Granada (UGR)
Digital.CSIC. Repositorio Institucional del CSIC
Consejo Superior de Investigaciones Científicas (CSIC)
Molecular Therapy: Nucleic Acids, Vol 34, Iss, Pp 102066-(2023)
Molecular Therapy-Nucleic Acids, 34, pp. 102066
Cavazza, A, Hendel, A, Bak, R O, Rio, P, Güell, M, Lainšček, D, Arechavala-Gomeza, V, Peng, L, Hapil, F Z, Harvey, J, Ortega, F G, Gonzalez-Martinez, C, Lederer, C W, Mikkelsen, K, Gasiunas, G, Kalter, N, Gonçalves, M A F V, Petersen, J, Garanto, A, Montoliu, L, Maresca, M, Seemann, S E, Gorodkin, J, Mazini, L, Sanchez, R, Rodriguez-Madoz, J R, Maldonado-Pérez, N, Laura, T, Schmueck-Henneresse, M, Maccalli, C, Grünewald, J, Carmona, G, Kachamakova-Trojanowska, N, Miccio, A, Martin, F, Turchiano, G, Cathomen, T, Luo, Y, Tsai, S Q & Benabdellah, K 2023, ' Progress and harmonization of gene editing to treat human diseases : Proceeding of COST Action CA21113 GenE-HumDi ', Molecular Therapy Nucleic Acids, vol. 34, 102066 . https://doi.org/10.1016/j.omtn.2023.102066
Cavazza, A, Hendel, A, Bak, R O, Rio, P, Güell, M, Lainšček, D, Arechavala-Gomeza, V, Peng, L, Hapil, F Z, Harvey, J, Ortega, F G, Gonzalez-Martinez, C, Lederer, C W, Mikkelsen, K, Gasiunas, G, Kalter, N, Gonçalves, M A F V, Petersen, J, Garanto, A, Montoliu, L, Maresca, M, Seemann, S E, Gorodkin, J, Mazini, L, Sanchez, R, Rodriguez-Madoz, J R, Maldonado-Pérez, N, Laura, T, Schmueck-Henneresse, M, Maccalli, C, Grünewald, J, Carmona, G, Kachamakova-Trojanowska, N, Miccio, A, Martin, F, Turchiano, G, Cathomen, T, Luo, Y, Tsai, S Q, Benabdellah, K & COST Action CA21113 2023, 'Progress and harmonization of gene editing to treat human diseases : Proceeding of COST Action CA21113 GenE-HumDi', Molecular Therapy Nucleic Acids, vol. 34, 102066, pp. 102066. https://doi.org/10.1016/j.omtn.2023.102066, https://doi.org/10.1016/j.omtn.2023.102066

Perez-Iturralde, A.; Belleli, A.; Morgan, C.; Chen, J.; Koudrina, A.; Nazareth, D.; Parate, H.; Garreta-Celemin, C. L.; Chandra, D.; Mesa, S.; Lainscek, D.; Osredkar, D.; Samaco, R.; Gonzalez Hernandez, A.; Mirosevic, S.; Lisowski, L.

HUMAN GENE THERAPY; FEB 1 2025, 36 3-4, pE148-pE149, 2p.

Plaper T; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI-1000, Ljubljana, Slovenia.; Merljak E; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI-1000, Ljubljana, Slovenia.; Fink T; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI-1000, Ljubljana, Slovenia.; Satler T; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI-1000, Ljubljana, Slovenia.; Interdisciplinary doctoral study of biomedicine, Medical Faculty, University of Ljubljana, 1000, Ljubljana, Slovenia.; Ljubetič A; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI-1000, Ljubljana, Slovenia.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI-1000, Ljubljana, Slovenia.; Jazbec V; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI-1000, Ljubljana, Slovenia.; Interdisciplinary doctoral study of biomedicine, Medical Faculty, University of Ljubljana, 1000, Ljubljana, Slovenia.; Benčina M; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI-1000, Ljubljana, Slovenia.; Centre for Technologies of Gene and Cell Therapy, Hajdrihova 19, SI-1000, Ljubljana, Slovenia.; Stevanoska S; Department of knowledge technologies, Jožef Stefan Institute, Jamova cesta 39, 1000, Ljubljana, Slovenia.; Džeroski S; Department of knowledge technologies, Jožef Stefan Institute, Jamova cesta 39, 1000, Ljubljana, Slovenia.; Jerala R; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI-1000, Ljubljana, Slovenia. roman.jerala@ki.si.; Centre for Technologies of Gene and Cell Therapy, Hajdrihova 19, SI-1000, Ljubljana, Slovenia. roman.jerala@ki.si.

Publisher: Nature Publishing Group Country of Publication: England NLM ID: 101661034 Publication Model: Electronic Cited Medium: Print ISSN: 2056-5968 (Print) Linking ISSN: 20565968 NLM ISO Abbreviation: Cell Discov Subsets: PubMed not MEDLINE

Cavazza A; Molecular and Cellular Immunology Section, Department of Infection, Immunity & Inflammation, UCL Great Ormond Street Institute of Child Health, University College London, 20 Guilford Street, London WC1N 1DZ, UK.; Department of Medical and Surgical Sciences for Children and Adults, University of Modena and Reggio Emilia School of Medicine, Via del Pozzo 71, 41125 Modena, Italy.; Molina-Estévez FJ; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.; Fundación para la Investigación Biosanitaria de Andalucía Oriental, Alejandro Otero (FIBAO), Avda. de Madrid 15, 18012 Granada, Spain.; Biosanitary Research Institute of Granada (ibs. GRANADA), University of Granada, Av. de Madrid, 15, Beiro, 18012 Granada, Spain.; Reyes ÁP; Department of Regeneration and Cell Therapy, Andalusian Molecular Biology and Regenerative Medicine Centre (CABIMER), Avda. Americo Vespucio, 24, 41092 Seville, Spain.; Ronco V; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.; Naseem A; Molecular and Cellular Immunology Section, Department of Infection, Immunity & Inflammation, UCL Great Ormond Street Institute of Child Health, University College London, 20 Guilford Street, London WC1N 1DZ, UK.; Malenšek Š; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Graduate School of Biomedicine, University of Ljubljana, Kongresni trg, 1000 Ljubljana, Slovenia.; Pečan P; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Graduate School of Biomedicine, University of Ljubljana, Kongresni trg, 1000 Ljubljana, Slovenia.; Santini A; Imagine Institute, UMR 163 INSERM, 24 Bd du Montparnasse, 75015 Paris, France.; Paris City University, 45 Rue des Saints-Pères, 75006 Paris, France.; Heredia P; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.; Department of Anatomy and Human Embryology, Faculty of Medicine, University of Granada, Avenida de la Investigación 11, 18016 Granada, Spain.; Aguilar-González A; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.; Biosanitary Research Institute of Granada (ibs. GRANADA), University of Granada, Av. de Madrid, 15, Beiro, 18012 Granada, Spain.; Department of Medicinal & Organic Chemistry and Excellence Research Unit of 'Chemistry applied to Bio-medicine and the Environment, ' Faculty of Pharmacy, University of Granada, Campus de Cartuja s/n, 18071 Granada, Spain.; Boulaiz H; Biosanitary Research Institute of Granada (ibs. GRANADA), University of Granada, Av. de Madrid, 15, Beiro, 18012 Granada, Spain.; Department of Anatomy and Human Embryology, Faculty of Medicine, University of Granada, Avenida de la Investigación 11, 18016 Granada, Spain.; Ni Q; Department of Diagnostic Radiology, Yong Loo Lin School of Medicine, National University of Singapore, Singapore 117597, Singapore.; Cortijo-Gutierrez M; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.; Pavlovic K; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.; Herrera I; Department of Hematology, Reina Sofía University Hospital, Av. Menéndez Pidal, Poniente Sur, 14004 Córdoba, Spain.; Maimonides Institute of Biomedical Research in Cordoba (IMIBIC), Cell Therapy, Av. Menéndez Pidal, Poniente Sur, 14004 Córdoba, Spain.; de la Cerda B; Department of Regeneration and Cell Therapy, Andalusian Molecular Biology and Regenerative Medicine Centre (CABIMER), Avda. Americo Vespucio, 24, 41092 Seville, Spain.; Garcia-Tenorio EM; Centro de Biología Molecular Severo Ochoa UAM-CSIC, IUBM, CIBERER, IDIPAZ, Universidad Autónoma de Madrid, C. de Pedro Rico, 6, Fuencarral-El Pardo, 28029 Madrid, Spain.; Richard E; Centro de Biología Molecular Severo Ochoa UAM-CSIC, IUBM, CIBERER, IDIPAZ, Universidad Autónoma de Madrid, C. de Pedro Rico, 6, Fuencarral-El Pardo, 28029 Madrid, Spain.; Granados-Principal S; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.; Biosanitary Research Institute of Granada (ibs. GRANADA), University of Granada, Av. de Madrid, 15, Beiro, 18012 Granada, Spain.; Department of Biochemistry and Molecular Biology 2, Faculty of Pharmacy, University of Granada, Campus de Cartuja s/n, 18071 Granada, Spain.; López-Márquez A; Neuromuscular Unit, Institut de Recerca Sant Joan de Déu, Hospital Sant Joan de Déu, C. de Sta. Rosa, 39, 08950 Barcelona, Spain.; Biomedical Research Network on Rare Diseases (CIBERER), C. de Melchor Fernández Almagro, 3, Fuencarral-El Pardo, 28029 Madrid, Spain.; Department of Genetics, Microbiology and Statistics, University of Barcelona, Gran Via de les Corts Catalanes, 585, L'Eixample, 08007 Barcelona, Spain.; Köber M; Biomedical Research Network on Bioengineering, Biomaterials and Nanomedicine (CIBER-BBN), C/ Monforte de Lemos 3-5, Pabellón 11, Planta 0, 28029 Madrid, Spain.; Institut de Ciència de Materials de Barcelona (ICMAB-CSIC), Campus UAB, Universitat Autònoma de Barcelona, 08193 Bellaterra, Barcelona, Spain.; Stojanovic M; Institute for Biological Research 'Siniša Stanković', University of Belgrade, Bulevar despota Stefana 142, 10060 Belgrade, Serbia.; Vidaković M; Institute for Biological Research 'Siniša Stanković', University of Belgrade, Bulevar despota Stefana 142, 10060 Belgrade, Serbia.; Santos-Garcia I; Department of Neurosciences, Biogipuzkoa Health Research Institute, Paseo Dr. Begiristain, s/n, 20014 San Sebastián, Gipuzkoa, Spain.; Blázquez L; Department of Neurosciences, Biogipuzkoa Health Research Institute, Paseo Dr. Begiristain, s/n, 20014 San Sebastián, Gipuzkoa, Spain.; CIBERNED, ISCIII CIBER, Carlos III Institute, Spanish Ministry of Sciences and Innovation), Av. de Monforte de Lemos, 5, Fuencarral-El Pardo, 28029 Madrid, Spain.; Ikerbasque, Basque Foundation for Science, Euskadi Pl., 5, Abando, 48009 Bilbao, Biscay, Spain.; Haughton E; Institute of Developmental & Regenerative Medicine, University of Oxford, Campus, Old Rd, Roosevelt Dr, Headington, Oxford OX3 7TY, UK.; Yan D; Institute of Developmental & Regenerative Medicine, University of Oxford, Campus, Old Rd, Roosevelt Dr, Headington, Oxford OX3 7TY, UK.; Nuffield Department of Women's and Reproductive Health, University of Oxford, John Radcliffe Hospital, Oxford OX3 9DU, UK.; Sánchez-Martín RM; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.; Biosanitary Research Institute of Granada (ibs. GRANADA), University of Granada, Av. de Madrid, 15, Beiro, 18012 Granada, Spain.; Department of Medicinal & Organic Chemistry and Excellence Research Unit of 'Chemistry applied to Bio-medicine and the Environment, ' Faculty of Pharmacy, University of Granada, Campus de Cartuja s/n, 18071 Granada, Spain.; Mazini L; Technological, Medical and Academic Park (TMAP), N°109, Abdelkrim Elkhatabi, Bd Abdelkrim Al Khattabi, Marrakech 40000, Morocco.; Aseguinolaza GG; DNA & RNA Medicine Division, Gene Therapy for Rare Diseases Department, Center for Applied Medical Research (CIMA), University of Navarra, IdisNA, Av. de Pío XII, 55, 31008 Pamplona, Navarra, Spain.; Vivet Therapeutics, Av. de Pío XII 31, 31008 Pamplona, Navarra, Spain.; Miccio A; Imagine Institute, UMR 163 INSERM, 24 Bd du Montparnasse, 75015 Paris, France.; Paris City University, 45 Rue des Saints-Pères, 75006 Paris, France.; Rio P; Biomedical Research Network on Rare Diseases (CIBERER), C. de Melchor Fernández Almagro, 3, Fuencarral-El Pardo, 28029 Madrid, Spain.; Division of Hematopoietic Innovative Therapies, CIEMAT, Av. Complutense, 40, Moncloa - Aravaca, 28040 Madrid, Spain.; Advanced Therapies Unit, IIS-Fundación Jimenez Diaz (IIS-FJD, UAM), Av. de los Reyes Católicos, 2, Moncloa - Aravaca, 28040 Madrid, Spain.; Desviat LR; Centro de Biología Molecular Severo Ochoa UAM-CSIC, IUBM, CIBERER, IDIPAZ, Universidad Autónoma de Madrid, C. de Pedro Rico, 6, Fuencarral-El Pardo, 28029 Madrid, Spain.; Gonçalves MAFV; Leiden University Medical Center, Department of Cell and Chemical Biology, Einthovenweg 20, 2333 ZC Leiden, the Netherlands.; Peng L; Aix-Marseille Universite, CNRS, Centre Interdisciplinaire de Nanoscience de Marseille, UMR 7325, 'Equipe Labellisee Ligue Ćontre le Cancer', Campus de Luminy, case 913, 13009 Marseille, France.; Jiménez-Mallebrera C; Neuromuscular Unit, Institut de Recerca Sant Joan de Déu, Hospital Sant Joan de Déu, C. de Sta. Rosa, 39, 08950 Barcelona, Spain.; Biomedical Research Network on Rare Diseases (CIBERER), C. de Melchor Fernández Almagro, 3, Fuencarral-El Pardo, 28029 Madrid, Spain.; Molina FM; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.; Biosanitary Research Institute of Granada (ibs. GRANADA), University of Granada, Av. de Madrid, 15, Beiro, 18012 Granada, Spain.; Department of Biochemistry and Molecular Biology III and Immunology, Faculty of Medicine, University of Granada, Avenida de la Investigación 11, 18016 Granada, Spain.; Gupta D; Institute of Developmental & Regenerative Medicine, University of Oxford, Campus, Old Rd, Roosevelt Dr, Headington, Oxford OX3 7TY, UK.; Department of Laboratory Medicine, Karolinska Institutet, Alfred Nobels allé 8, 141 52 Huddinge, Sweden.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Centre for Technologies of Gene and Cell Therapy, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; EN-FIST Centre of Excellence, Trg Osvobodilne fronte 13, 1000 Ljubljana, Slovenia.; Luo Y; Department of Biomedicine, Aarhus University, 8000 Aarhus C, Denmark.; Steno Diabetes Center Aarhus, Aarhus University Hospital, 8200 Aarhus N, Denmark.; Benabdellah K; Department of Genomic Medicine, Pfizer-University of Granada-Andalusian Regional Government Centre for Genomics and Oncological Research (GENYO), Av. de la Ilustración, 114, 18016 Granada, Spain.

Publisher: Cell Press Country of Publication: United States NLM ID: 101581621 Publication Model: eCollection Cited Medium: Print ISSN: 2162-2531 (Print) Linking ISSN: 21622531 NLM ISO Abbreviation: Mol Ther Nucleic Acids Subsets: PubMed not MEDLINE

Mlakar, T.; Mikolic, V.; Zalig, J. Pantovic; Sever, M.; Lainscek, D.; Jerala, R.

HUMAN GENE THERAPY; FEB 1 2025, 36 3-4, pE426-pE427, 2p.

Lainscek, D.; Malensek, S.; Golob-Urbanc, A.; Orehek, S.; Keber, M. Mancek; Esih, H.; Forstneric, V.; Pantovic-Zalig, J.; Bencina, M.; Bester, R.; Potzer, U.; Jerala, R.

HUMAN GENE THERAPY; FEB 1 2025, 36 3-4, pE331-pE332, 2p.

Esih, H.; Mezgec, K.; Billmeier, M.; Malensek, S.; Bencina, M.; Grilc, B.; Bele, M.; Vidmar, S.; Gasperlin, M.; Zidarn, M.; Zupanc, T. Lejko; Morgan, T.; Jordan, I.; Sandig, V.; Schroedel, S.; Thirion, C.; Protzer, U.; Wagner, R.; Lainscek, D.; Jerala, R.

HUMAN GENE THERAPY; FEB 1 2025, 36 3-4, pE337-pE338, 2p.

Maruna, M.; Susjan-Leite, P.; Lainscek, D.; Iturralde, A. Perez; Lisowski, L.; Mirosevic, S.; Jerala, R.

HUMAN GENE THERAPY; FEB 1 2025, 36 3-4, pE291-pE292, 2p.

Marolt Presen D; Centre for the Technologies of Gene and Cell Therapy, National Institute of Chemistry, Hajdrihova 19, SI1000 Ljubljana, Slovenia.; Lainšček D; Centre for the Technologies of Gene and Cell Therapy, National Institute of Chemistry, Hajdrihova 19, SI1000 Ljubljana, Slovenia.; Department for Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI1000 Ljubljana, Slovenia.; Kinghorn J; Translational Research Office, Innovation & Enterprise, University College London, Gower Street, London WC1E 6BT, UK.; Sebestyen Z; Center for Translational Immunology, University Medical Center Utrecht, Utrecht University, Utrecht, The Netherlands.; Kuball J; Center for Translational Immunology, University Medical Center Utrecht, Utrecht University, Utrecht, The Netherlands.; Department of Hematology, University Medical Center Utrecht, Utrecht University, Utrecht, The Netherlands.; Amini L; Berlin Center for Advanced Therapies, Charité-Universitätsmedizin Berlin, Berlin, Germany.; Berlin Institute of Health - Center for Regenerative Therapies, Charité-Universitätsmedizin Berlin, Berlin, Germany.; Reinke P; Berlin Center for Advanced Therapies, Charité-Universitätsmedizin Berlin, Berlin, Germany.; Berlin Institute of Health - Center for Regenerative Therapies, Charité-Universitätsmedizin Berlin, Berlin, Germany.; Fuchs A; Center for Regenerative Therapies Dresden, Center for Molecular and Cellular Bioengeneering, Technische Universität Dresden, Dresden, Germany.; Jerala R; Centre for the Technologies of Gene and Cell Therapy, National Institute of Chemistry, Hajdrihova 19, SI1000 Ljubljana, Slovenia.; Department for Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI1000 Ljubljana, Slovenia.; Benčina M; Centre for the Technologies of Gene and Cell Therapy, National Institute of Chemistry, Hajdrihova 19, SI1000 Ljubljana, Slovenia.; Department for Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, SI1000 Ljubljana, Slovenia.

Publisher: Elsevier B.V. on behalf of Research Network of Computational and Structural Biotechnology Country of Publication: Netherlands NLM ID: 101585369 Publication Model: eCollection Cited Medium: Print ISSN: 2001-0370 (Print) Linking ISSN: 20010370 NLM ISO Abbreviation: Comput Struct Biotechnol J Subsets: PubMed not MEDLINE

Rodriguez Lavado, J; SESTITO, STEFANIA ENZA; CIGHETTI, ROBERTO; Aguilar Moncayo, E; Oblak, A; Lainšček, D; Jiménez Blanco, J; García Fernández, J; Ortiz Mellet, C; Jerala, R; CALABRESE, VALENTINA; PERI, FRANCESCO

idUS. Depósito de Investigación de la Universidad de Sevilla
Universidad de Sevilla (US)
instname
Digital.CSIC. Repositorio Institucional del CSIC

Rihtar E; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Fink T; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia; Centre for Technologies of Gene and Cell Therapy, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Lebar T; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Lainšček D; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia; Centre for Technologies of Gene and Cell Therapy, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Kolenc Ž; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Polajnar LK; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia.; Jerala R; Department of Synthetic Biology and Immunology, National Institute of Chemistry, Hajdrihova 19, 1000 Ljubljana, Slovenia; Centre for Technologies of Gene and Cell Therapy, Hajdrihova 19, 1000 Ljubljana, Slovenia. Electronic address: roman.jerala@ki.si.

Publisher: Cell Press Country of Publication: United States NLM ID: 101676030 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2451-9448 (Electronic) Linking ISSN: 24519448 NLM ISO Abbreviation: Cell Chem Biol Subsets: MEDLINE

Osredkar, D.; Moultrie, F.; Mirosevic, S.; Lilien, C.; Zakelj, N.; Gosar, D.; Lainscek, D.; Perez-Iturralde, A.; Lisowski, L.; Jerala, R.; Servais, L.

HUMAN GENE THERAPY; FEB 1 2025, 36 3-4, pE238-pE238, 1p.