학술논문
'학술논문'
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1~10
Academic Journal
Vishwanathan, V.; Chidambaranathan, S.; Biggar, W. Douglas; McAdam, Laura C.; Mah, Jean K.; Tulinius, Mar; Cnaan, Avital; Morgenroth, Lauren P.; Leshner, Robert; TesiRocha, Carolina; Thangarajh, Mathula; Duong, Tina; Kornberg, Andrew; Ryan, Monique; Nevo, Yoram; Dubrovsky, Alberto; Clemens, Paula R.; Abdel-Hamid, Hoda; Connolly, Anne M.; Pestronk, Alan; Teasley, Jean; Bertorini, Tulio E.; Webster, Richard; Kolski, Hanna; Kuntz, Nancy; Driscoll, Sherilyn; Bodensteiner, John B.; Carlo, Jose; Gorni, Ksenija; Lotze, Timothy; Day, John W.; Karachunski, Peter; Henricson, Erik K.; Abresch, Richard T.; Joyce, Nanette C.; McDonald, Craig M.; Landfeldt, Erik; Iff, Joel; Henricson, Erik
In Value in Health October 2021 24(10):1490-1498
Academic Journal
Vishwanathan, Vijay; Chidambaranathan, S; Biggar, W. Douglas; McAdam, Laura C.; Mah, Jean K.; Tulinius, Mar; Cnaan, Avital; Morgenroth, Lauren P.; Leshner, Robert; Tesi-Rocha, Carolina; Thangarajh, Mathula; Duong, Tina; Kornberg, Andrew; Ryan, Monique; Nevo, Yoram; Dubrovsky, Alberto; Clemens, Paula R.; Abdel-Hamid, Hoda; Connolly, Anne M.; Pestronk, Alan; Teasley, Jean; Bertorin, Tulio E.; Webster, Richard; Kolski, Hanna; Kuntz, Nancy; Driscoll, Sherilyn; Bodensteiner, John B.; Carlo, Jose; Gorni, Ksenija; Lotze, Timothy; Day, John W.; Karachunski, Peter; Henricson, Erik K.; Abresch, Richard T.; Joyce, Nanette C.; McDonald, Craig M.; McDonald, Craig M; Henricson, Erik K; Abresch, Richard T; Joyce, Nanette C; Hu, Fengming; Clemens, Paula R; Hoffman, Eric P; Gordish-Dressman, Heather
In The Lancet 3-9 February 2018 391(10119):451-461
Academic Journal
Alfano, Lindsay N; Eagle, Michelle; James, Meredith K; Lowes, Linda; Mayhew, Anna; Mazzone, Elena S; Nelson, Leslie; Rose, Kristy J; Abdel-Hamid, Hoda Z; Apkon, Susan D; Barohn, Richard J; Bertini, Enrico; Bloetzer, Clemens; de Vaud, Lausanne Canton; Butterfield, Russell J; Chabrol, Brigitte; Chae, Jong-Hee; Jongno-gu, Daehak-ro; Comi, Giacomi Pietro; Darras, Basil T; Dastgir, Jahannaz; Desguerre, Isabelle; Escobar, Raul G; Finanger, Erika; Guglieri, Michela; Hughes, Imelda; Iannaccone, Susan T; Jones, Kristi J; Karachunski, Peter; Kudr, Martin; Lotze, Timothy; Mah, Jean K; Mathews, Katherine; Nevo, Yoram; Parsons, Julie; Péréon, Yann; de Queiroz Campos Araujo, Alexandra Prufer; Renfroe, J Ben; de Resende, Maria Bernadete Dutra; Ryan, Monique; Selby, Kathryn; Tennekoon, Gihan; Vita, Giuseppe; McDonald, Craig M; Campbell, Craig; Torricelli, Ricardo Erazo; Finkel, Richard S; Flanigan, Kevin M; Goemans, Nathalie; Heydemann, Peter; Kaminska, Anna; Kirschner, Janbernd; Muntoni, Francesco; Osorio, Andrés Nascimento; Schara, Ulrike; Sejersen, Thomas; Shieh, Perry B; Sweeney, H Lee; Topaloglu, Haluk; Tulinius, Már; Vilchez, Juan J; Voit, Thomas; Wong, Brenda; Elfring, Gary; Kroger, Hans; Luo, Xiaohui; McIntosh, Joseph; Ong, Tuyen; Riebling, Peter; Souza, Marcio; Spiegel, Robert J; Peltz, Stuart W; Mercuri, Eugenio
In The Lancet 23-29 September 2017 390(10101):1489-1498
Academic Journal
Lodge, Samantha; Litton, Edward; Gray, Nicola; Ryan, Monique; Millet, Oscar; Fear, Mark; Raby, Edward; Currie, Andrew; Wood, Fiona; Holmes, Elaine; Wist, Julien; Nicholson, Jeremy K.
Academic Journal
Lee Sweeney, H; Finanger, Erika; Neil Knierbein, Erin; Wagner, Kathryn; Mathews, Katherine; Marks, Warren; Statland, Jeffrey; Nance, Jessica; McMillan, Hugh; McCullagh, Gary; Tian, Cuixia; Ryan, Monique; ORourke, Declan; Müller-Felber, Wolfgang; Tulinius, Mar; Burnette, W; Nguyen, Cam-Tu; Vijayakumar, Kayal; Johannsen, Jessika; Phan, Han; Eagle, Michelle; MacDougall, James; Mancini, Maria; Donovan, Joanne; Finkel, Richard; McDonald, Craig
Journal of Neuromuscular Diseases. 8(5)
Academic Journal
Heier, Christopher; Zhang, Aiping; Nguyen, Nhu; Tully, Christopher; Panigrahi, Aswini; Gordish-Dressman, Heather; Pandey, Sachchida; Guglieri, Michela; Ryan, Monique; Clemens, Paula; Thangarajh, Mathula; Webster, Richard; Smith, Edward; Connolly, Anne; Karachunski, Peter; Tulinius, Mar; Harper, Amy; Mah, Jean; Fiorillo, Alyson; Chen, Yi-Wen; McDonald, Craig
Journal of Personalized Medicine. 10(4)
Academic Journal
Smith, Edward; Conklin, Laurie; Hoffman, Eric; Clemens, Paula; Mah, Jean; Finkel, Richard; Guglieri, Michela; Tulinius, Mar; Nevo, Yoram; Ryan, Monique; Webster, Richard; Castro, Diana; Kuntz, Nancy; Kerchner, Laurie; Morgenroth, Lauren; Arrieta, Adrienne; Shimony, Maya; Jaros, Mark; Shale, Phil; Gordish-Dressman, Heather; Hagerty, Laura; Dang, Utkarsh; Damsker, Jesse; Schwartz, Benjamin; Mengle-Gaw, Laurel; McDonald, Craig
PLoS Medicine. 17(9)
Academic Journal
Hoffman, Eric; Schwartz, Benjamin; Mengle-Gaw, Laurel; Smith, Edward; Castro, Diana; Mah, Jean; Kuntz, Nancy; Finkel, Richard; Guglieri, Michela; Bushby, Katharine; Tulinius, Mar; Nevo, Yoram; Ryan, Monique; Webster, Richard; Smith, Andrea; Morgenroth, Lauren; Arrieta, Adrienne; Shimony, Maya; Siener, Catherine; Jaros, Mark; Shale, Phil; McCall, John; Nagaraju, Kanneboyina; van den Anker, John; Conklin, Laurie; Cnaan, Avital; Gordish-Dressman, Heather; Damsker, Jesse; Clemens, Paula; McDonald, Craig
Neurology. 93(13)
Academic Journal
Yau, Andrew; Fear, Mark W; Gray, Nicola; Ryan, Monique; Holmes, Elaine; Nicholson, Jeremy K; Whiley, Luke; Wood, Fiona M
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