학술논문
Risdiplam in Spinal Muscular Atrophy: Safety Profile and Use Through The Early Access to Medicine Scheme for the Paediatric Cohort in Great Britain
Document Type
Article
Author
Source
In: Journal of Neuromuscular Diseases . (Journal of Neuromuscular Diseases, 5 March 2024, 11(2):361-368)
Subject
Language
English
ISSN
22143602
22143599
22143599