학술논문
A splice-switching oligonucleotide treatment ameliorates glycogen storage disease type 1a in mice with G6PC c.648G>T
Document Type
Article
Author
Ito, K.; Kamisato, C.; Nagase, H.; Tsuji, S.; Nishizawa, T.; Kakuta, M.; Takaishi, K.; Tajima, G.; Tsumura, M.; Okada, S.; Iwamoto, M.; Sekiguchi, Y.; Numata, Y.; Masuda, T.; Onishi, Y.; Koizumi, M.; Watanabe, K.; Yabe, Y.; Kanki, S.; Oitate, M.; Fujieda, Y.; Sogawa, Y.; Goto, K.; Nakamura, H.; Matsuo, M.
Source
In: Journal of Clinical Investigation . (Journal of Clinical Investigation, 10 December 2023, 133(23))
Subject
Language
English
ISSN
15588238
00219738
00219738