학술논문
Outcomes of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome
Document Type
Article
Author
Labrosse, R.; Chu, J.I.; Armant, M.A.; Kareddy, N.; Frelinger, A.L.; Coenen-van der Spek, J.; Miggelbrink, A.; Fiorini, C.; Fong, J.; Jaroslavsky, J.; Whangbo, J.S.; London, W.B.; Williams, D.A.; Pai, S.-Y.; Everett, J.K.; Adhikari, H.; Cantu, V.A.; Karadeniz, D.F.; Reddy, S.; Roche, A.M.; Bushman, F.D.; Pellin, D.; Dansereau, C.; Mackinnon, B.; Morris, E.; Koo, S.M.; Henderson, L.A.; Notarangelo, L.D.; O'Connell, A.E.; Biswas, A.; Snapper, S.B.; Berry, C.C.; Li, Q.-Z.; Zhu, C.; Baris, S.; Ozen, A.; Karakoc-Aydiner, E.; Despotovic, J.M.; Forbes Satter, L.R.; Saitoh, A.; Aizawa, Y.; King, A.; Nguyen, M.A.T.; Vu, V.D.U.; Galy, A.
Source
In: Blood . (Blood, 12 October 2023, 142(15):1281-1296)
Subject
Language
English
ISSN
15280020
00064971
00064971