학술논문

Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy
Document Type
Article
Author
Obici, L.Ajroud-Driss, S.Lin, K.-P.Berk, J.L.Gillmore, J.D.Kale, P.Koike, H.Danese, D.Aldinc, E.Chen, C.Vest, J.Adams, D.Wixner, J.Backlund, R.Pilebro, B.Anan, I.Edbom, F.Ekman, A.Arvidsson, S.Englund, U.Söderberg, K.Nordh, E.Uneus, E.Samuelsson, K.Nilzen, A.Press, R.Bilecen, M.Coelho, T.Novais, M.Rodrigues, P.Martins da Silva, A.Cardoso, I.Rodrigues, C.Ramalho, J.Martins, H.Silva, M.Guimaraes, N.Perez, J.Reis, A.H.Monte, J.Ferreira, N.Alves, C.Cardoso, M.Teixeira, R.Conceição, I.Lamas, F.Oliveira Santos, M.Campos, C.de Azevedo Coutinho, C.Castro, J.Castro, I.Silva, D.Gonçalves, S.Di Buduo, E.Sforzini, C.Mussinelli, R.Rosti, V.Lozza, A.Racchi, A.Sabatelli, M.Luigetti, M.Bisogni, G.Romano, A.Guglielmino, V.Di Paolantonio, A.Bernardo, D.Vita, G.Mazzeo, A.Russo, M.Pareyson, D.Calabrese, D.Fenu, S.Saveri, P.Nienhuis, H.Bokhorst, G.Roos, C.Couperus, M.De Jong, G.Brunger, A.Drost, G.Lange, F.Colauto, A.Waddington-Cruz, M.Abreu, A.Pedrosa, R.C.Gervais de Santa Rosa, R.Dias, M.Rakotondratafika, F.Echaniz-Laguna, A.Cauquil, C.Labeyrie, C.Beaudonnet, G.Boubrit, Y.Gaouar, A.Bourenane, H.Attarian, S.Yahia, E.K.Verschueren, A.Grapperon, A.-M.Delmont, E.Planté-Bordeneuve, V.Vervoitte, L.Ayache, S.S.Le Corvoisier, P.Arrouasse, R.Gendre, T.Abou Chakra, L.Focsénéanu, C.Barau, C.Sole, G.Belin, L.Violleau, M.H.Duval-Bontemps, F.Massie, R.Dong, X.Muñoz-Beamud, F.García Garrido, S.Borrachero, C.Gragera Martinez, A.Galán Dávila, L.Palacios, M.Vicente, L.M.Perez de Isla, L.Casasnovas, C.Díez López, C.Fabra, E.González-Costello, J.Guerrero, S.Yun Viladomat, S.Martinez, Y.Velez-Santamaria, V.Nedkova-Hristova, V.Garcia Pavia, P.Gonzalez Segovia, A.De Frutos, F.Gonzalez-Lopez, E.Dominguez, F.Escobar-López, L.E.Cabrera-Romero, E.Sánchez Gismera, P.de la Iglesia, M.Martinez Valle, F.Mazuela Aguila, G.Lorite, K.Raguer, N.Suñé, P.Piera, P.Ortega, C.Aguilar, C.Gili, G.Schmidt, H.Langenstroer, C.Hüsing-Kabar, A.Kabar, I.Schilling, M.Friebel, F.Tepasse, P.-R.Birklein, F.Firros, M.Escolano-Lozano, F.Brueckner, C.Bahnam, V.Kaku, M.C.Lau, K.H.V.Wiesman, J.Grogan, M.Miller, S.Frantz, J.Schmidt, D.C.AbouEzzeddine, O.Miller, W.Lin, G.Gertz, M.Dispenzieri, A.Brannagan, T.Fayerman, R.DuVerger, E.Cabrera, J.Maurer, M.S.Ulane, C.M.Weimer, L.H.Tsang, S.Shije, J.Carberry, N.Thu, S.S.Quan, D.Blume, B.Overcash, J.S.Pu, H.Lee, K.Chu, H.Zepeda, K.Waters, M.Vuong, T.Coskun, D.Quillin, K.Davis, A.Polydefkis, M.Ye, J.Li, X.Khoshnoodi, M.Vista, G.Chung, T.H.Watt, M.Tsottles, D.Masri, A.Carlson, D.Drachman, B.Divito, P.Mathelier, H.Shanks, M.Maslowski, K.Khella, S.Pieretti, J.Joslin, B.Schmidt, E.Freimer, M.Agriesti, J.Barroso, F.Picone, F.Lautre, A.Orellana, L.Du, W.Felius, J.González-Duarte, A.Cardenas Soto, K.Traub, R.Chopra, M.Chao, C.-C.Hsu, C.-H.Tsai, L.-K.Lee, M.-J.Su, J.-J.Hsieh, S.-T.Hsueh, H.-W.Chou, H.-C.Kim, B.-J.Kang, H.Min, J.-H.Jeon, E.-S.Chung, Y.H.Park, J.H.Oh, J.Jeong, H.J.Tournev, I.Zhelyazkova, S.Misumi, Y.Sakamoto, Y.Hashimoto, N.Misumi, Y.Takahashi, A.Ueda, M.Masuda, T.Ueda, A.Katsuno, M.Tajima, K.Sumi, M.Hasegawa, F.Okumura, T.Iijima, M.Fukami, Y.Ito, D.Kishimoto, Y.Kazuta, T.Kato, K.Mouri, N.Furukawa, S.Nishi, R.Sekijima, Y.Ito, K.Kato, N.Kishida, D.Mochizuki, H.Okada, K.Ohashi, K.Ikenaka, K.Nakamori, M.Kinoshita, M.Mapalo, B.R.Law, S.Chacko, L.Lachmann, H.Cohen, O.Razvi, Y.S.K.Varughese, S.Martinez-Naharro, A.Orrell, R.Fontana, M.Rannigan, L.Louth, S.Zamba-Papanicolaou, E.Charalamnibous, D.Manneh, R.A.Kleopa, K.Christodoulides, T.Frangos, S.Galganski-Cleanthous, M.Gaglia, E.Smoleski, I.Kkolou, E.Ploutarchou, A.Hanghiuc, M.Chroidou, G.Stylianou, O.Krokou, A.Zannetou, I.Kastritis, E.Papadopoulou, D.Spinasas, I.Bakalis, P.Kanellias, N.Fotiou, D.Dialoupi, I.Migko, M.Gavriatopoulou, M.Low, S.-C.Taylor, M.Stewart, G.Knight, H.Vucic, S.Carroll, A.Silsby, M.Suan, D.Gibbs, S.Corfield, C.Jakicic, S.Jina, H.Ting, S.Wong, S.Q.Mollee, P.McKinley, L.Abro, E.Korczyk, D.Remiche, G.Alaerts, N.De Veylder, F.Claeys, K.Debien, E.Cremers, J.D’hondt, A.De Wel, B.
Source
In: Neurology and Therapy. (Neurology and Therapy, October 2023, 12(5):1759-1775)
Subject
Language
English
ISSN
21936536
21938253