학술논문
A framework for individualized splice-switching oligonucleotide therapy
Document Type
Article
Author
Kim, J.; Woo, S.; de Gusmao, C.M.; Friedman, D.A.; El Achkar, C.M.; Zhao, B.; Chin, D.H.; DiDonato, R.L.; Nguyen, M.A.; Nakayama, T.; Hu, C.A.; Soucy, A.; Riccardi, O.; Dash, Z.; Faour, K.N.W.; Bush, L.W.; Suslovitch, V.; Lentucci, C.; Lee, E.A.; Yu, T.W.; Patterson, A.; Berde, C.B.; Kuniholm, A.; Thornton, J.K.; Margus, B.; Cornelissen, L.; Donado, C.; Park, P.J.; Philippakis, A.A.
Source
In: Nature . (Nature, 27 July 2023, 619(7971):828-836)
Subject
Language
English
ISSN
14764687
00280836
00280836