학술논문

Long-term safety and efficacy of velmanase alfa treatment in children under 6 years of age with alpha-mannosidosis: A phase 2, open label, multicenter study
Document Type
Article
Source
In: Journal of Inherited Metabolic Disease. (Journal of Inherited Metabolic Disease, July 2023, 46(4):705-719)
Subject
Language
English
ISSN
15732665
01418955