학술논문
Long-term efficacy and safety of sapropterin in patients who initiated sapropterin at < 4 years of age with phenylketonuria: results of the 3-year extension of the SPARK open-label, multicentre, randomised phase IIIb trial
Document Type
Article
Author
Source
In: Orphanet Journal of Rare Diseases . (Orphanet Journal of Rare Diseases, December 2021, 16(1))
Subject
Language
English
ISSN
17501172