학술논문

Nusinersen versus sham control in infantile-onset spinal muscular atrophy
Document Type
Article
Author
Finkel, R.S.Mercuri, E.Darras, B.T.Zhong, Z.J.Gheuens, S.Farwell, W.Connolly, A.M.Kuntz, N.L.Kirschner, J.Chiriboga, C.A.Montes, J.De Vivo, D.C.Saito, K.Servais, L.Tizzano, E.Topaloglu, H.Tulinius, M.Glanzman, A.M.Bishop, K.Bennett, C.F.Schneider, E.Bradley, W.G.Schroth, M.K.Bodensteriner, J.B.Davis, C.S.Shell, R.Hen, J.Austin, E.D.Aziz-Zaman, S.Cappell, J.Constantinescu, A.Cruz, R.Dastgir, J.Dunaway, S.Engelstad, K.Gormley, M.Holuba La Marca, N.Khandji, A.Kramer, S.Marra, J.Ortiz-Miller, C.Popolizio, M.Salazar, R.Sanabria, L.Weimer, L.Anand, P.Gadeken, R.Golumbek, P.T.Siener, C.Zaidman, C.M.Al-Ghamdi, F.Berde, C.Ghosh, P.Graham, R.Harrington, T.Koka, A.Laine, R.Liew, W.Mirek, E.Ordonez, G.Pasternak, A.Quigley, J.Sethna, N.Souris, M.Szelag, H.Wand, L.Day, J.W.D'Souza, G.Duong, T.T.Gee, R.Kitsuwa-Lowe, J.McFall, D.Patnaik, S.Paulose, S.Perez, J.Proud, C.Purse, B.Ramamurthi, R.J.Sakamuri, S.Sampson, J.Sanjanwala, B.Tesi Rocha, A.C.Watson, K.Welsh, L.Pena, L.D.M.Case, L.Coates, J.DeArmey, S.Homi, M.M.Milleson, C.Nelson, N.Ross, A.Smith, E.Taicher, B.Wootton, J.Finanger, E.Benjamin, D.Frank, A.Roberts, C.Russman, B.Zilke, K.Berry, D.Civitello, M.Cook, D.Endsley, J.D.Johnson, C.Kasper, M.Leon, W.Lim, A.O'Reardon, K.Sigurdardottir, L.Y.Turner, J.Weber-Guzman, F.Zinn, M.Iannaccone, S.T.Castro, D.Cowie, M.Farrow-Gillespie, A.Herbert, A.Kauk, M.McElroy, D.Miller, N.Nelson, L.Smith, L.Spain, T.Trest, S.Johnson, N.Butterfield, R.DiBella, D.Mayne, K.Newcomb, T.M.Rausch, N.Blomgren, C.Choi, H.W.Epstein, L.Goldman, S.Krosschell, K.Krueger, J.Kurz, J.Rao, V.Parsons, J.Allen, V.Bielsky, A.Booker, K.Camuto, A.Carry, T.Fuhr, P.Gibbons, M.Janas, J.Johnson, H.Kelly, C.Lord-Halvorson, L.S.Nicolarsen, S.Shea, S.Tran, V.VanderVeen, G.Yang, M.Zimmerman, C.Shieh, P.Parziale, N.Rao, L.Said, J.W.Shu, F.Skura, C.Staudt, L.Tennekoon, G.Adang, L.Brandsema, J.Chadehumbe, M.Flickinger, J.Kichula, E.Stanford, D.Toms, M.Zigmont, J.Oskoui, M.Arpin, S.Dinunzio, P.Ingelmo, P.M.Poulin, C.Rivera, G.Sabapathy, C.Srour, M.Turgeon-Desilet, S.Zielinski, D.Selby, K.King, C.Lee, J.Michoulas, A.Roland, E.Vajsar, J.Chau, V.Dowling, J.Haldenby, R.Miki, M.So, S.Pascual Pascual, S.I.Martinez Bermejo, A.Epinosa Garcia, S.Garcia Guixot, S.Martinez Moreno, M.M.del Pilar Tirado Requero, M.del Mar Garcia Romero, M.Aguilar, C.Munell Casadesus, F.Gomez Garcia de la Banda, M.B.Gallardo, M.Gili, G.Alavarez Molinero, M.de Los Angeles Tormos Munoz, M.Palacios, N.J.Planas Pascual, B.del Mar Melendez Plumed, M.Rucian, A.F.Toro Tamargo, E.Gratacos Vinola, M.Borell, S.Eckenweiler, M.Krüger, M.Pechmann, A.Rippberger, B.Stein, S.Vogt, S.Wider, S.Schara, U.Andres, B.Della Marina, A.Ganfuss, A.Jachertz, P.Koelbel, H.Rupprich, K.Schroers, E.S.Sponemann, N.Bruno, C.Fiorillo, C.Garaventa, A.Lanteri, P.Lanzillotta, V.Manzitti, C.Pedermonte, M.Tacchetti, P.Trucco, F.Zuffi, A.De Sanctis, R.Fanelli, L.Luigetti, M.Palermo, C.Pane, M.Piastra, M.Sivo, S.Gargaun, E.Gidaro, T.Gilabert, S.Léger, P.L.Le Moing, A.G.Lilien, C.Mayer, M.Ollievier, Q.Rambaud, J.Taytard, J.Vialle, R.Voit, T.Muntoni, F.D'Argenzio, L.Lister, PH.Manzur, A.Pisco Domingos, J.Ramsey, D.Ricotti, V.Schottlaender, L.Scoto, M.Scuplak, S.M.Selby, V.Straub, V.Baily, S.Bertoli, M.Mayhew, A.G.Lofra, R.M.Murphy, A.Wood, C.Darin, N.Eldblom, J.Kimber, E.Kroksmark, A.K.Lindstedt, A.Michael, E.Sofou, K.Deconinck, N.Christiaens, A.Coppens, S.DeCock, K.De Vos voor, E.Dorban, F.Gilbert, G.Rooze, S.Tahon, V.Van Coster, R.Van Der Looven, R.Vanlander, A.Vens, D.Verhelst, H.Wenderickx, B.Wittevrongel, S.Farrar, M.Berthon-Jones, N.Doumit, M.A.Herbert, K.J.Kandula, T.Morrison, M.O'Brien, J.Richardson, S.Ferreira Sampaio, H.A.Teoh, H.L.Ryan, M.Carroll, K.M.De Valle, K.L.Villano, D.Woodcock, I.Yiu, E.M.Ardicli, D.Gunbey, C.Haliloglu, V.G.Karaduman, A.A.Konuskan, B.Yildiz Sarikaya, F.G.Serdaroglu, E.Tanyildiz, M.Temucin, C.M.Yildirim, M.Yilmaz, O.T.Arakawa, R.Chiba, Y.Eto, K.Hirasawa, K.Ikai, T.Ito, S.Ito, Y.Kaburagi, Y.Kaneko, H.Matsumaru, S.Matsushima, N.Mizuochi, K.Nagata, S.Nakatsukasa, H.Nishikawa, A.Otani, Y.Sato, T.Shichiji, M.Sugimoto, K.Takeshita, A.Yanagishita, T.Yamauchi, A.Takeshima, Y.Fujino, T.Fukuda, N.Lee, T.Oriyama, K.Shibano, T.Shimomura, H.Tachikawa, T.Tanaka, Y.Taniguchi, N.Chae, J.H.Choi, S.A.Chun, S.M.Jo, H.Kim, H.Kim, S.Y.Lee, J.S.Lim, B.C.Shin, H.I.Son, W.S.Chan, S.Chung, A.C.Yan, C.S.Stella, C.Joseph, C.K.W.Ng, C.S.Alvin, H.C.C.Janice, I.J.K.Wendy, L.W.M.Chui-San, M.N.Ki, N.Y.Shun, T.N.Connie, W.Y.Virginia, W.C.Yvonne, Y.Jong, Y.J.Chen, T.H.Chou, P.C.Chou, Y.H.Chung, H.W.Hsu, J.H.Ju, Y.H.Liang, W.C.Shih, H.H.Wang, H.Y.Wu, Y.C.Zeng, Y.S.
Source
In: New England Journal of Medicine. (New England Journal of Medicine, 2 November 2017, 377(18):1723-1732)
Subject
Language
English
ISSN
15334406
00284793