학술논문
Mapping the differences in care for 5,000 Spinal Muscular Atrophy patients, a survey of 24 national registries in North America, Australasia and Europe
Document Type
Article
Author
Bladen, C.L.; Thompson, R.; Rafferty, K.; Straub, V.; Bushby, K.; Lochmüller, H.; Jackson, J.M.; Garland, C.; Wegel, C.; Ambrosini, A.; Pisano, P.; Walter, M.C.; Schreiber, O.; Lusakowska, A.; Kostera-Pruszczyk, A.; Van Der Pol, L.; Wadman, R.I.; Gredal, O.; Karaduman, A.; Topaloglu, H.; Yilmaz, O.; Matyushenko, V.; Rasic, V.M.; Kosac, A.; Karcagi, V.; Garami, M.; Herczegfalvi, A.; Monges, S.; Moresco, A.; Chertkoff, L.; Chamova, T.; Guergueltcheva, V.; Butoianu, N.; Craiu, D.; Korngut, L.; Campbell, C.; Haberlova, J.; Strenkova, J.; Alejandro, M.; Ortiz, G.G.; Enriquez, G.V.G.; Jimenez, A.; Rodrigues, M.; Roxburgh, R.; Dawkins, H.; Youngs, L.; Lahdetie, J.; Angelkova, N.; Saugier-Veber, P.; Cuisset, J.-M.; Bloetzer, C.; Jeannet, P.-Y.; Klein, A.; Nascimento, A.; Tizzano, E.; Salgado, D.; Beroud, C.; Mercuri, E.; Sejersen, T.; Kirschner, J.; Verschuuren, J.; Jedrzejowska, M.
Source
In: Journal of Neurology . (Journal of Neurology, January 2014, 261(1):152-163)
Subject
Language
English
ISSN
03405354
14321459
14321459