학술논문
A promoterless AAV6.2FF-based lung gene editing platform for the correction of surfactant protein B deficiency
Document Type
Article
Author
Thomas, Sylvia P.; Domm, Jakob M.; van Vloten, Jacob P.; Xu, Liqun; Vadivel, Arul; Yates, Jacob G.E.; Pei, Yanlong; Ingrao, Joelle; van Lieshout, Laura P.; Jackson, Sergio R.; Minott, Jessica A.; Achuthan, Adithya; Mehrani, Yeganeh; McAusland, Thomas M.; Zhang, Wei; Karimi, Khalil; Vaughan, Andrew E.; de Jong, Jondavid; Kang, Martin H.; Thebaud, Bernard; Wootton, Sarah K.
Source
In Molecular Therapy 6 December 2023 31(12):3457-3477
Subject
Language
ISSN
1525-0016