학술논문
Safety and efficacy of ganaxolone in patients with CDKL5 deficiency disorder: results from the double-blind phase of a randomised, placebo-controlled, phase 3 trial
Document Type
Article
Author
Belousova, Elena; Belyaev, Oleg; Ben-Zeev, Bruria; Brunklaus, Andreas; Ciliberto, Michael A.; Darra, Francesca; Davis, Ronald; De Giorgis, Valentina; Doronina, Olga; Fahey, Michael; Guerrini, Renzo; Heydemann, Peter; Khaletskaya, Olga; Lisewski, Pawel; Marsh, Eric D.; Moosa, Ahsan N.; Perry, Scott; Philip, Sunny; Rajaraman, Rajsekar R.; Renfroe, Ben; Saneto, Russell P.; Scheffer, Ingrid E.; Sogawa, Yoshimi; Suter, Bernhardt; Sweney, Matthew T.; Tarquinio, Daniel; Veggiotti, Pierangelo; Wallace, Geoff; Weisenberg, Judy; Wilfong, Angus; Wirrell, Elaine C.; Zafar, Muhammad; Zolnowska, Marta; Knight, Elia M Pestana ; Amin, Sam; Bahi-Buisson, Nadia; Benke, Tim A; Cross, J Helen; Demarest, Scott T; Olson, Heather E; Specchio, Nicola; Fleming, Thomas R; Aimetti, Alex A; Gasior, Maciej; Devinsky, Orrin
Source
In The Lancet Neurology May 2022 21(5):417-427
Subject
Language
ISSN
1474-4422