학술논문
Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study
Document Type
Article
Author
Klopstock, Thomas ; Tricta, Fernando; Neumayr, Lynne; Karin, Ivan; Zorzi, Giovanna; Fradette, Caroline; Kmieć, Tomasz; Büchner, Boriana; Steele, Hannah E; Horvath, Rita; Chinnery, Patrick F; Basu, Anna; Küpper, Clemens; Neuhofer, Christiane; Kálmán, Bernadette; Dušek, Petr; Yapici, Zuhal; Wilson, Ian; Zhao, Feng; Zibordi, Federica; Nardocci, Nardo; Aguilar, Christine; Hayflick, Susan J; Spino, Michael; Blamire, Andrew M; Hogarth, Penelope; Vichinsky, Elliott
Source
In The Lancet Neurology July 2019 18(7):631-642
Subject
Language
ISSN
1474-4422