학술논문
Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease.
Document Type
Article
Author
Source
Frontiers in Genetics; 3/24/2023, Vol. 14, p01-15, 15p
Subject
Language
ISSN
16648021
Abstract
Copyright of Frontiers in Genetics is the property of Frontiers Media S.A. and its content may not be copied or emailed to multiple sites or posted to a listserv without the copyright holder's express written permission. However, users may print, download, or email articles for individual use. This abstract may be abridged. No warranty is given about the accuracy of the copy. Users should refer to the original published version of the material for the full abstract. (Copyright applies to all Abstracts.)