학술논문
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Matthias Sauter; Elena Belousova; Mirjana P. Benedik; Tom Carter; Vincent Cottin; Paolo Curatolo; Maria Dahlin; Lisa D’Amato; Guillaume B. d’Augères; Petrus J. de Vries; José C. Ferreira; Martha Feucht; Carla Fladrowski; Christoph Hertzberg; Sergiusz Jozwiak; John A. Lawson; Alfons Macaya; Ruben Marques; Rima Nabbout; Finbar O’Callaghan; Jiong Qin; Valentin Sander; Seema Shah; Yukitoshi Takahashi; Renaud Touraine; Sotiris Youroukos; Bernard Zonnenberg; Anna Jansen; J. Chris Kingswood; the TOSCA investigators
Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-15 (2021)
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[AR] the TOSCA investigators
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