학술논문
'학술논문'
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1~10
Artificial microRNA suppresses C9ORF72variants and decreases toxic dipeptide repeat proteins in vivo
Periodical
Cabrera, Gabriela Toro; Meijboom, Katharina E.; Abdallah, Abbas; Tran, Helene; Foster, Zachariah; Weiss, Alexandra; Wightman, Nicholas; Stock, Rachel; Gendron, Tania; Gruntman, Alisha; Giampetruzzi, Anthony; Petrucelli, Leonard; Brown, Robert H.; Mueller, Christian
Gene Therapy; March 2024, Vol. 31 Issue: 3-4 p105-118, 14p
Academic Journal
Cabrera, Gabriela Toro; Meijboom, Katharina E.; Abdallah, Abbas; Tran, Helene; Foster, Zachariah; Weiss, Alexandra; Wightman, Nicholas; Stock, Rachel; Gendron, Tania; Gruntman, Alisha; Giampetruzzi, Anthony; Petrucelli, Leonard; Brown, Jr, Robert H.; Mueller, Christian
Gene Therapy. 31(3-4):105-118
Academic Journal
Cabrera, Gabriela Toro; Meijboom, Katharina E.; Abdallah, Abbas; Tran, Helene; Foster, Zachariah; Weiss, Alexandra; Wightman, Nicholas; Stock, Rachel; Gendron, Tania; Gruntman, Alisha; Giampetruzzi, Anthony; Petrucelli, Leonard; Brown, Robert H.; Mueller, Christian
Academic Journal
Quezada, Esteban; Cappelli, Claudio; Diaz, Iván; Jury, Nur; Wightman, Nicholas; Brown, Robert H.; Montecino, Martín; van Zundert, Brigitte
Academic Journal
Tran, Hélène; Moazami, Michael P.; Yang, Huiya; McKenna-Yasek, Diane; Douthwright, Catherine L.; Pinto, Courtney; Metterville, Jake; Shin, Minwook; Sanil, Nitasha; Dooley, Craig; Puri, Ajit; Weiss, Alexandra; Wightman, Nicholas; Gray-Edwards, Heather; Marosfoi, Miklos; King, Robert M.; Kenderdine, Thomas; Fabris, Daniele; Bowser, Robert; Watts, Jonathan K.; Brown, Jr, Robert H.
Nature Medicine. 28(1):117-124
Periodical
Tran, Hélène; Moazami, Michael P.; Yang, Huiya; McKenna-Yasek, Diane; Douthwright, Catherine L.; Pinto, Courtney; Metterville, Jake; Shin, Minwook; Sanil, Nitasha; Dooley, Craig; Puri, Ajit; Weiss, Alexandra; Wightman, Nicholas; Gray-Edwards, Heather; Marosfoi, Miklos; King, Robert M.; Kenderdine, Thomas; Fabris, Daniele; Bowser, Robert; Watts, Jonathan K.; Brown, Robert H.
Nature Medicine; 20210101, Issue: Preprints p1-8, 8p
Academic Journal
Cammack, Alexander J.; Atassi, Nazem; Hyman, Theodore; van den Berg, Leonard H.; Harms, Matthew; Baloh, Robert H.; Brown, Robert H.; van Es, Michael A.; Veldink, Jan H.; de Vries, Balint S.; Rothstein, Jeffrey D.; Drain, Caroline; Jockel-Balsarotti, Jennifer; Malcolm, Amber; Boodram, Sonia; Salter, Amber; Wightman, Nicholas; Hong Yu; Sherman, Alexander V.; Esparza, Thomas J.
Neurology; 10/22/2019, Vol. 93 Issue 17, pe1605-e1617, 13p
Academic Journal
Academic Journal
Cammack, Alexander J.; Atassi, Nazem; Hyman, Theodore; van den Berg, Leonard H.; Harms, Matthew; Baloh, Robert H.; Brown, Robert H.; van Es, Michael A.; Veldink, Jan H.; de Vries, Balint S.; Rothstein, Jeffrey D.; Drain, Caroline; Jockel-Balsarotti, Jennifer; Malcolm, Amber; Boodram, Sonia; Salter, Amber; Wightman, Nicholas; Yu, Hong; Sherman, Alexander V.; Esparza, Thomas J.; McKenna-Yasek, Diane; Owegi, Margaret A.; Douthwright, Catherine; McCampbell, Alexander; Ferguson, Toby; Cruchaga, Carlos; Cudkowicz, Merit; Miller, Timothy M.
Neurology. Oct 22, 2019 93(17):e1605-e1617
Academic Journal
Tran, Helene; Moazami, Michael P.; Yang, Huiya; McKenna-Yasek, Diane; Douthwright, Catherine L.; Pinto, Courtney; Metterville, Jake; Shin, Minwook; Sanil, Nitasha; Dooley, Craig; Puri, Ajit; Weiss, Alexandra; Wightman, Nicholas; Gray-Edwards, Heather; Marosfoi, Miklos; King, Robert M.; Kenderdine, Thomas; Fabris, Daniele; Bowser, Robert; Watts, Jonathan K.; Brown, Robert H., Jr.
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[AR] Wightman, Nicholas
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