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Twice weekly dosing with Sebelipase alfa (Kanuma®) rescues severely ill infants with Wolman disease.
Academic Journal
de Castro, María José; Jones, Simon A; de las Heras, Javier; Sánchez-Pintos, Paula; Couce, María L; Colón, Cristóbal; Crujeiras, Pablo; Unceta, María; Church, Heather; Brammeier, Kathryn; Yee, Wu Hoi; Cooper, James; López de Frutos, Laura; Serrano-Gonzalo, Irene; Camba, María José; White, Fiona J.; Holmes, Victoria; Ghosh, Arunabha
Academic Journal
Porro, Francesco; Orsenigo, Simone; Abeli, Thomas; Mondoni, Andrea; Corli, Anna; White, Fiona J.; Lodetti, Silvano; Tomaselli, Marcello; Petraglia, Alessandro; Carbognani, Michele; Gualmini, Matteo; Forte, T'ai G. W.; Erschbamer, Brigitta; Nicklas, Lena; Carnicero, Pau; Mallaun, Martin; Unterluggauer, Peter; Stanisci, Angela; Giancola, Carmen; di Martino, Luciano
Academic Journal
Potter, Jane E.; Petts, Gemma; Ghosh, Arunabha; White, Fiona J.; Kinsella, Jane L.; Hughes, Stephen; Roberts, Jane; Hodgkinson, Adam; Brammeier, Kathryn; Church, Heather; Merrigan, Christine; Hughes, Joanne; Evans, Pamela; Campbell, Helen; Bonney, Denise; Newman, William G.; Bigger, Brian W.; Broomfield, Alexander; Jones, Simon A.; Wynn, Robert F.
Academic Journal
Halligan, Rebecca; White, Fiona J.; Schwahn, Bernd; Stepien, Karolina M.; Jaman, Nazreen Kamarus; Mcsweeney, Mel; Kitchen, Steve; Gribben, Joanna; Dawson, Charlotte; Lewis, Katherine; Cregeen, David; Mundy, Helen; Santra, Saikat
JIMD Reports. May 2021, Vol. 59 Issue 1, p52, 8 p.
Academic Journal
Wood, Georgina; Pinto, Alex; Evans, Sharon; Daly, Anne; Adams, Sandra; Costelloe, Susie; Gribben, Joanna; Ellerton, Charlotte; Emm, Anita; Firman, Sarah; Ford, Suzanne; French, Moira; Gaff, Lisa; Giuliano, Emily; Hill, Melanie; Hunjan, Inderdip; Newby, Camille; Mackenzie, Allison; Pereira, Rachel; Prescott, Celine; Robertson, Louise; Seabert, Heidi; Skeath, Rachel; Tapley, Simon; Terry, Allyson; Tooke, Alison; van Wyk, Karen; White, Fiona J.; White, Lucy; Woodall, Alison; Rocha, Julio Cesar; MacDonald, Anita
Academic Journal
Porro, Francesco; Orsenigo, Simone; Abeli, Thomas; Mondoni, Andrea; Corli, Anna; White, Fiona J.; Lodetti, Silvano; Tomaselli, Marcello; Petraglia, Alessandro; Carbognani, Michele; Gualmini, Matteo; Forte, T'ai G. W.; Erschbamer, Brigitta; Nicklas, Lena; Carnicero, Pau; Mallaun, Martin; Unterluggauer, Peter; Stanisci, Angela; Giancola, Carmen; di Martino, Luciano; Barni, Elena; Oddi, Ludovica; di Cella, Umberto Morra; Gentili, Rodolfo; Dellavedova, Roberto; Adorni, Michele; Pauli, Harald; Rossi, Graziano
Academic Journal
International Journal of Adolescent Medicine and Health. 16(1):41-46
Academic Journal
The Journal of Pediatrics. Apr 01, 2000 136(4):545-547
Academic Journal
Journal of Inherited Metabolic Disease: Official Journal of the Society for the Study of Inborn Errors of Metabolism. June 2011 34(3):631-642
Periodical
Biochemical Society Transactions; October 1984, Vol. 12 Issue: 5 p791-792, 2p
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[AR] White, Fiona J.
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