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Onasemnogene abeparvovec in spinal muscular atrophy: an Australian experience of safety and efficacy
Academic Journal
Arlene M. D'Silva; Sandra Holland; Didu Kariyawasam; Karen Herbert; Peter Barclay; Anita Cairns; Suzanna C. MacLennan; Monique M. Ryan; Hugo Sampaio; Nicholas Smith; Ian R. Woodcock; Eppie M. Yiu; Ian E. Alexander; Michelle A. Farrar
Annals of Clinical and Translational Neurology, Vol 9, Iss 3, Pp 339-350 (2022)
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[AR] Sandra Holland
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