학술논문
'학술논문'
에서 검색결과 17건 | 목록
1~10
Academic Journal
McKay, Matthew; Urban, Barbara; Lund, Caroline; Froeter, Erin; LaCasse, Taylor; Mehalow, Adrienne; Gordon, Emily; Donahue, Leah Rae; Taft, Robert; Kutney, Peter; Dion, Stephanie; Goodwin, Leslie; Kales, Susan; Urban, Rachel; Palmer, Kristina; Pertuy, Fabien; Bitz, Deborah; Weber, Bruno; Goetz-Reiner, Patrice; Jacobs, Hughes; Le Marchand, Elise; El Amri, Amal; El Fertak, Leila; Ennah, Hamid; Ali-Hadji, Dalila; Ayadi, Abdel; Wattenhofer-Donze, Marie; Jacquot, Sylvie; André, Philippe; Birling, Marie-Christine; Pavlovic, Guillaume; Sorg, Tania; Morse, Iva; Benso, Frank; Stewart, Michelle E; Copley, Carol; Harrison, Jackie; Joynson, Samantha; Guo, Ruolin; Qu, Dawei; Spring, Shoshana; Yu, Lisa; Ellegood, Jacob; Morikawa, Lily; Shang, Xueyuan; Feugas, Pat; Creighton, Amie; Castellanos Penton, Patricia; Danisment, Ozge; Griggs, Nicola; Tudor, Catherine L; Green, Angela L; Icoresi Mazzeo, Cecilia; Siragher, Emma; Lillistone, Charlotte; Tuck, Elizabeth; Gleeson, Diane; Sethi, Debarati; Bayzetinova, Tanya; Burvill, Jonathan; Habib, Bishoy; Weavers, Lauren; Maswood, Ryea; Miklejewska, Evelina; Woods, Michael; Grau, Evelyn; Newman, Stuart; Sinclair, Caroline; Brown, Ellen; Ayabe, Shinya; Iwama, Mizuho; Murakami, Ayumi
Nature. 537(7621)
Aguila, Monica; Bellingham, James; Athanasiou, Dimitra; Bevilacqua, Dalila; Duran, Yanai; Maswood, Ryea; Parfitt, David A.; Iwawaki, Takao; Spyrou, Ioannis; Smith, Alexander J.; Ali, Robin R.; Cheetham, Michael E.
Human Molecular Genetics. 29(8):1310-1318
Academic Journal
kleine Holthaus, Sophia-Martha; Aristorena, Mikel; Maswood, Ryea; Semenyuk, Olha; Hoke, Justin; Hare, Aura; Smith, Alexander J.; Mole, Sara E.; Ali, Robin R.
Neonatal brain-directed gene therapy rescues a mouse model of neurodegenerative CLN6 Batten disease.
Academic Journal
Holthaus, Sophia-Martha kleine; Herranz-Martin, Saul; Massaro, Giulia; Aristorena, Mikel; Hoke, Justin; Hughes, Michael P.; Maswood, Ryea; Semenyuk, Olha; Basche, Mark; Shah, Amna Z.; Klaska, Izabela P.; Smith, Alexander J.; Mole, Sara E.; Rahim, Ahad A.; Ali, Robin R.
Human Molecular Genetics; 12/1/2019, Vol. 28 Issue 23, p3867-3879, 13p
Periodical
Wu, Jiahui; Bell, Oliver H.; Copland, David A.; Young, Alison; Pooley, John R.; Maswood, Ryea; Evans, Rachel S.; Khaw, Peng Tee; Ali, Robin R.; Dick, Andrew D.; Chu, Colin J.
Molecular Therapy; March 2020, Vol. 28 Issue: 3 p820-829, 10p
Periodical
kleine Holthaus, Sophia-Martha; Ribeiro, Joana; Abelleira-Hervas, Laura; Pearson, Rachael A.; Duran, Yanai; Georgiadis, Anastasios; Sampson, Robert D.; Rizzi, Matteo; Hoke, Justin; Maswood, Ryea; Azam, Selina; Luhmann, Ulrich F.O.; Smith, Alexander J.; Mole, Sara E.; Ali, Robin R.
Molecular Therapy; May 2018, Vol. 26 Issue: 5 p1343-1353, 11p
Academic Journal
Holthaus, Sophia-Martha Kleine; Aristorena, Mikel; Maswood, Ryea; Semenyuk, Olha; Hoke, Justin; Hare, Aura; Smith, Alexander J.; Mole, Sara E.; Ali, Robin R.
Academic Journal
Liu, Wenfei; Geard, Amy; Massaro, Giulia; Hughes, Michael Paul; Aristorena, Mikel; Semenyuk, Olha; Maswood, Ryea; Smith, Alexander J.; Ali, Robin R.; Mole, Sara; Rahim, Ahad A.
Academic Journal
Dickinson, Mary E.; Flenniken, Ann M.; Ji, Xiao; Teboul, Lydia; Wong, Michael D.; White, Jacqueline K.; Meehan, Terrence F.; Weninger, Wolfgang J.; Westerberg, Henrik; Adissu, Hibret; Baker, Candice N.; Bower, Lynette; Brown, James M.; Caddle, L. Brianna; Chiani, Francesco; Clary, Dave; Cleak, James; Daly, Mark J.; Denegre, James M.; Doe, Brendan; Dolan, Mary E.; Edie, Sarah M.; Fuchs, Helmut; Gailus-Durner, Valerie; Galli, Antonella; Gambadoro, Alessia; Gallegos, Juan; Guo, Shiying; Horner, Neil R.; Hsu, Chih-Wei; Johnson, Sara J.; Kalaga, Sowmya; Keith, Lance C.; Lanoue, Louise; Lawson, Thomas N.; Lek, Monkol; Mark, Manuel; Marschall, Susan; Mason, Jeremy; McElwee, Melissa L.; Newbigging, Susan; Nutter, Lauryl M. J.; Peterson, Kevin A.; Ramirez-Solis, Ramiro; Rowland, Douglas J.; Ryder, Edward; Samocha, Kaitlin E.; Seavitt, John R.; Selloum, Mohammed; Szoke-Kovacs, Zsombor; Tamura, Masaru; Trainor, Amanda G.; Tudose, Ilinca; Wakana, Shigeharu; Warren, Jonathan; Wendling, Olivia; West, David B.; Wong, Leeyean; Yoshiki, Atsushi; McKay, Matthew; Urban, Barbara; Lund, Caroline; Froeter, Erin; LaCasse, Taylor; Mehalow, Adrienne; Gordon, Emily; Donahue, Leah Rae; Taft, Robert; Kutney, Peter; Dion, Stephanie; Goodwin, Leslie; Kales, Susan; Urban, Rachel; Palmer, Kristina; Pertuy, Fabien; Bitz, Deborah; Weber, Bruno; Goetz-Reiner, Patrice; Jacobs, Hughes; Le Marchand, Elise; El Amri, Amal; El Fertak, Leila; Ennah, Hamid; Ali-Hadji, Dalila; Ayadi, Abdel; Wattenhofer-Donze, Marie; Jacquot, Sylvie; Andr, Philippe; Birling, Marie-Christine; Pavlovic, Guillaume; Sorg, Tania; Morse, Iva; Benso, Frank; Stewart, Michelle E.; Copley, Carol; Harrison, Jackie; Joynson, Samantha; Guo, Ruolin; Qu, Dawei; Spring, Shoshana; Yu, Lisa; Ellegood, Jacob; Morikawa, Lily; Shang, Xueyuan; Feugas, Pat; Creighton, Amie; Castellanos Penton, Patricia; Danisment, Ozge; Griggs, Nicola; Tudor, Catherine L.; Green, Angela L.; Icoresi Mazzeo, Cecilia; Siragher, Emma; Lillistone, Charlotte; Tuck, Elizabeth; Gleeson, Diane; Sethi, Debarati; Bayzetinova, Tanya; Burvill, Jonathan; Habib, Bishoy; Weavers, Lauren; Maswood, Ryea; Miklejewska, Evelina; Woods, Michael; Grau, Evelyn; Newman, Stuart; Sinclair, Caroline; Brown, Ellen; Ayabe, Shinya; Iwama, Mizuho; Murakami, Ayumi; MacArthur, Daniel G.; Tocchini-Valentini, Glauco P.; Gao, Xiang; Flicek, Paul; Bradley, Allan; Skarnes, William C.; Justice, Monica J.; Parkinson, Helen E.; Moore, Mark; Wells, Sara; Braun, Robert E.; Svenson, Karen L.; de Angelis, Martin Hrabe; Herault, Yann; Mohun, Tim; Mallon, Ann-Marie; Henkelman, R. Mark; Brown, Steve D. M.; Adams, David J.; Lloyd, K. C. Kent; McKerlie, Colin; Beaudet, Arthur L.; Buan, Maja; Murray, Stephen A.
Nature. September 22, 2016, Vol. 537 Issue 7621, 508
Academic Journal
Holthaus, Sophia-Martha Kleine; Ribeiro, Joana; Abelleira-Hervas, Laura; Pearson, Rachael A.; Duran, Yanai; Georgiadis, Anastasios; Sampson, Robert D.; Rizzi, Matteo; Hoke, Justin; Maswood, Ryea; Azam, Selina; Luhmann, Ulrich F. O.; Smith, Alexander J.; Mole, Sara E.; Ali, Robin R.
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[AR] Maswood, Ryea
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