학술논문
'학술논문'
에서 검색결과 15건 | 목록
1~10
Academic Journal
Natan Bar-Chama; Bakri Elsheikh; Channa Hewamadduma; Carol Jean Guittari; Ksenija Gorni; Lutz Mueller
Neurology and Therapy, Vol 13, Iss 4, Pp 933-947 (2024)
Academic Journal
Claudia A. Chiriboga; Claudio Bruno; Tina Duong; Dirk Fischer; Eugenio Mercuri; Janbernd Kirschner; Anna Kostera-Pruszczyk; Birgit Jaber; Ksenija Gorni; Heidemarie Kletzl; Imogen Carruthers; Carmen Martin; Francis Warren; Renata S. Scalco; Kathryn R. Wagner; Francesco Muntoni; the JEWELFISH Study Group
Neurology and Therapy, Vol 12, Iss 5, Pp 1799-1801 (2023)
Academic Journal
Claudia A. Chiriboga; Claudio Bruno; Tina Duong; Dirk Fischer; Eugenio Mercuri; Janbernd Kirschner; Anna Kostera-Pruszczyk; Birgit Jaber; Ksenija Gorni; Heidemarie Kletzl; Imogen Carruthers; Carmen Martin; Francis Warren; Renata S. Scalco; Kathryn R. Wagner; Francesco Muntoni; the JEWELFISH Study Group
Neurology and Therapy, Vol 12, Iss 2, Pp 543-557 (2023)
Academic Journal
Claude Cances; Dmitry Vlodavets; Giacomo Pietro Comi; Riccardo Masson; Maria Mazurkiewicz-Bełdzińska; Kayoko Saito; Edmar Zanoteli; Angela Dodman; Muna El-Khairi; Ksenija Gorni; Isaac Gravestock; Janine Hoffart; Renata S. Scalco; Basil T. Darras; the ANCHOVY Working Group
Orphanet Journal of Rare Diseases, Vol 17, Iss 1, Pp 1-11 (2022)
Academic Journal
Mélanie Annoussamy; Andreea M. Seferian; Aurore Daron; Yann Péréon; Claude Cances; Carole Vuillerot; Liesbeth De Waele; Vincent Laugel; Ulrike Schara; Teresa Gidaro; Charlotte Lilien; Jean‐Yves Hogrel; Pierre Carlier; Emmanuel Fournier; Linda Lowes; Ksenija Gorni; Myriam Ly‐Le Moal; Nicole Hellbach; Timothy Seabrook; Christian Czech; Ricardo Hermosilla; Laurent Servais; the NatHis‐SMA study group
Annals of Clinical and Translational Neurology, Vol 8, Iss 2, Pp 359-373 (2021)
Academic Journal
Tina Duong; Hannah Staunton; Jessica Braid; Aurelie Barriere; Ben Trzaskoma; Ling Gao; Tom Willgoss; Rosangel Cruz; Nicole Gusset; Ksenija Gorni; Sharan Randhawa; Lida Yang; Carole Vuillerot
Frontiers in Neurology, Vol 12 (2022)
Academic Journal
Dylan Trundell; Stephanie Le Scouiller; Ksenija Gorni; Timothy Seabrook; Carole Vuillerot; the SMA MFM Study Group
Neurology and Therapy, Vol 9, Iss 2, Pp 575-584 (2020)
Academic Journal
PLoS ONE, Vol 15, Iss 9, p e0238786 (2020)
Academic Journal
Andrea Barp; Luca Bello; Luisa Politano; Paola Melacini; Chiara Calore; Angela Polo; Sara Vianello; Gianni Sorarù; Claudio Semplicini; Boris Pantic; Antonella Taglia; Ester Picillo; Francesca Magri; Ksenija Gorni; Sonia Messina; Gian Luca Vita; Giuseppe Vita; Giacomo P Comi; Mario Ermani; Vincenzo Calvo; Corrado Angelini; Eric P Hoffman; Elena Pegoraro
PLoS ONE, Vol 10, Iss 10, p e0141240 (2015)
Academic Journal
Springer, PharmacoEconomics. 40(1):91-102
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[AR] Ksenija Gorni
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