학술논문

Phase 1 Danon Disease Results: The First Single Dose Intravenous (IV) Gene Therapy (RP-A501) With Recombinant Adeno-Associated Virus (AAV9:LAMP2B) for a Monogenic Cardiomyopathy
Document Type
Journal
Source
CIRCULATION; NOV 8 2022, 146 2p. Supplement: 1
Subject
Language
English
ISSN
15244539