학술논문
Outcomes of Gene Therapy for beta Thalassemia Major via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral beta A T87Q Globin Vector
Document Type
Journal
Author
Cavazzana, M.; Ribeil, J. A.; Payen, E.; Suarez, F.; Negre, O.; Beuzard, Y.; Touzot, F.; Cavallesco, R.; Lefrere, F.; Chretien, S.; Bourget, P.; Monpoux, F.; Pondarre, C.; Neven, B.; Bushman, F.; Schmidt, M.; von Kalle, C.; Sandler, L.; Soni, S.; Ryu, B.; Kutner, R.; Veres, G.; Finer, M.; Blanche, S.; Hermine, O.; Hacein-Bey-Abina, Salima; Leboulch, P.
Source
Subject
Language
English
ISSN
15577422