학술논문
Safety and Efficacy of CTX001 in Patients with Transfusion-Dependent beta-Thalassemia and Sickle Cell Disease: Early Results from the Climb THAL-111 and Climb SCD-121 Studies of Autologous CRISPR-CAS9-Modified CD34+Hematopoietic Stem and Progenitor Cells
Document Type
Journal
Author
Frangoul, Haydar; Bobruff, Yael; Cappellini, Maria Domenica; Corbacioglu, Selim; Fernandez, Christine Marie; De la Fuente, Josu; Grupp, Stephan A.; Handgretinger, Rupert; Ho, Tony W.; Imren, Suzan; Kattamis, Antonis; Lekstrom-Himes, Julie; Locatelli, Franco; Lu, Yimeng; Mapara, Markus Y.; De Montalembert, Mariane; Mulcahey, Sarah D.; Rondelli, Damiano; Shanbhag, Niraj; Sheth, Sujit; Soni, Sandeep; Steinberg, Martin H.; Weinstein, Michael J.; Wu, John K.; Wall, Donna
Source
Subject
Language
English
ISSN
15280020