학술논문

AAV-mediated PEX1 gene augmentation improves visual function in the PEX1-Gly844Asp mouse model for mild Zellweger spectrum disorder
Document Type
Journal
Source
MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT; DEC 10 2021, 23 p225-p240, 16p.
Subject
Language
English
ISSN
23290501