학술논문
Efficacy and safety of sapropterin before and during pregnancy: Final analysis of the Kuvan Adult Maternal Paediatric European Registry (KAMPER) maternal and Phenylketonuria Developmental Outcomes and Safety (PKUDOS) PKU-MOMs sub-registries
Document Type
Journal
Author
Feillet, Francois; Ficicioglu, Can; Lagler, Florian B.; Longo, Nicola; Muntau, Ania C.; Burlina, Alberto; Trefz, Friedrich K.; van Spronsen, Francjan J.; Arnoux, Jean-Baptiste; Lindstrom, Kristin; Lilienstein, Joshua; Clague, Gillian E.; Rowell, Richard; Burton, Barbara K.; KAMPER Investigator; PKUDOS Investigator
Source
Subject
Language
English
ISSN
15732665