학술논문
Onasemnogene Abeparvovec in Presymptomatic Spinal Muscular Atrophy (SMA): SPRINT Study Update in Children with Three Copies of SMN2
Document Type
Journal
Author
Strauss, Kevin; Muntoni, Francesco; Farrar, Michelle; Saito, Kayoko; Mendell, Jerry; Servais, Laurent; McMillan, Hugh; Finkel, Richard; Swoboda, Kathryn; Kwon, Jennifer; Zaidman, Craig; Chiriboga, Claudia; Lannaccone, Susan; Krueger, Jena; Parsons, Julie; Shieh, Perry; Kavanagh, Sarah; Chand, Deepa; Tauscher-Wisniewski, Sitra; McGill, Bryan; Macek, Thomas
Source
Subject
Language
English
ISSN
1526632X