학술논문

Preclinical Proof-of-Concept: A Novel Hybrid Gene Therapy Approach to Treat Severe Early-Onset Ornithine Transcarbamylase Deficiency
Document Type
Journal
Source
MOLECULAR THERAPY; MAY 1 2023, 31 4, p68-p69, 2p. Supplement: 1
Subject
Language
English
ISSN
15250024