학술논문
Sustained Efficacy, Safety, and Improved Quality of Life in Adult and Pediatric Patients with Transfusion-Dependent beta-Thalassemia up to 9 Years Post Treatment with Betibeglogene Autotemcel (Beti-cel)
Document Type
Journal
Author
Thompson, Alexis A.; Olson, Timothy S.; Walters, Mark C.; Porter, John B.; Schneiderman, Jennifer; Hongeng, Suradej; Kulozik, Andreas; Cavazzana, Marina; Sauer, Martin G.; Thrasher, Adrian J.; Thuret, Isabelle; Lal, Ashutosh; Rasko, John E. J.; Yannaki, Evangelia; Ali, Shamshad; Tao, Gloria; Thakar, Himal L.; Deora, Ami; Gruppioni, Katiana; Colvin, Richard A.; Locatelli, Franco; Kwiatkowski, Janet L.
Source
Subject
Language
English
ISSN
15280020