학술논문
Intracerebral Gene Therapy Using AAVrh.10-hARSA Recombinant Vector to Treat Patients with Early-Onset Forms of Metachromatic Leukodystrophy: Preclinical Feasibility and Safety Assessments in Nonhuman Primates
Document Type
Journal
Author
Zerah, Michel; Piguet, Francoise; Colle, Marie-Anne; Raoul, Sylvie; Deschamps, Jack-Yves; Deniaud, Johan; Gautier, Benoit; Toulgoat, Frederique; Bieche, Ivan; Laurendeau, Ingrid; Sondhi, Dolan; Souweidane, Mark M.; Cartier-Lacave, Nathalie; Moullier, Philippe; Crystal, Ronald G.; Roujeau, Thomas; Sevin, Caroline; Aubourg, Patrick
Source
Subject
Language
English
ISSN
23248645