학술논문

Efficacy and safety of subcutaneous prophylaxis with dalcinonacog alfa in adults with haemophilia B
Document Type
article
Source
Haemophilia. 27(4)
Subject
Biomedical and Clinical Sciences
Clinical Sciences
Hematology
Clinical Trials and Supportive Activities
Clinical Research
Evaluation of treatments and therapeutic interventions
6.1 Pharmaceuticals
Adult
Blood Coagulation Tests
Factor IX
Half-Life
Hemophilia A
Hemophilia B
Humans
Male
clinical trial
dalcinonacog alfa
factor IX
haemophilia B
immunogenicity
prophylaxis
subcutaneous
Cardiovascular System & Hematology
Clinical sciences
Language
Abstract
AimPhase 2b study to assess efficacy, safety, thrombogenicity, immunogenicity and tolerability with 28 days of daily dosing of subcutaneous (SQ) dalcinonacog alfa as prophylaxis for haemophilia B (HB).MethodsAdult males with a confirmed diagnosis of congenital HB (factor IX [FIX] activity