학술논문
Response of Patients with Transfusion-Dependent β-Thalassemia (TDT) to Betibeglogene Autotemcel (beti-cel; LentiGlobin for β-Thalassemia) Gene Therapy Based on HBB Genotype and Disease Genetic Modifiers
Document Type
Abstract
Author
Walters, Mark C.; Chui, David H.K.; Farrell, John J ; Lal, Ashutosh; Locatelli, Franco; Kwiatkowski, Janet L.; Porter, John B. ; Sauer, Martin G.; Thuret, Isabelle ; Hongeng, Suradej; Kulozik, Andreas E. ; Thrasher, Adrian J. ; Yannaki, Evangelia ; Yang, Julia ; Whitney, Dustin ; Petrusich, Alexandria ; Colvin, Richard A. ; Thompson, Alexis A.
Source
In Blood 5 November 2020 136 Supplement 1:1-3
Subject
Language
ISSN
0006-4971