학술논문

Efficacy and safety of ataluren in patients with nonsense-mutation cystic fibrosis not receiving chronic inhaled aminoglycosides: The international, randomized, double-blind, placebo-controlled Ataluren Confirmatory Trial in Cystic Fibrosis (ACT CF)
Document Type
Article
Source
In Journal of Cystic Fibrosis July 2020 19(4):595-601
Subject
Language
ISSN
1569-1993