학술논문

Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in adults with non-transfusion dependent α-thalassaemia or β-thalassaemia: an open-label, multicentre, phase 2 study
Document Type
Article
Source
In The Lancet 13-19 August 2022 400(10351):493-501
Subject
Primary Research
Articles
Language
ISSN
0140-6736