학술논문

CAS9-MEDIATED PRECISE AND TEMPLATE-FREE GENE EDITING OF A MUSCULAR DYSTROPHY FOUNDER MUTATION: FROM SINGLE EDITING AND OFF-TARGET ANALYSIS TO DOUBLE EDITING AND CLINICAL TRANSLATION
Document Type
Abstract
Source
In Cytotherapy June 2024 26(6) Supplement:S29-S29
Subject
Language
ISSN
1465-3249