학술논문
P.374 - AVXS-101 phase 1 gene therapy clinical trial in SMA Type 1: patients treated early with the proposed therapeutic dose were able to sit unassisted at a younger age
Document Type
Abstract
Author
Source
In Neuromuscular Disorders October 2017 27 Supplement 2:S208-S209
Subject
Language
ISSN
0960-8966