학술논문
First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated Achromatopsia
Document Type
Article
Author
Michaelides, Michel; Hirji, Nashila; Wong, Sui Chien; Besirli, Cagri G.; Zaman, Serena; Kumaran, Neruban; Georgiadis, Anastasios; Smith, Alexander J.; Ripamonti, Caterina; Gottlob, Irene; Robson, Anthony G.; Thiadens, Alberta; Henderson, Robert H.; Fleck, Penny; Anglade, Eddy; Dong, Xiangwen; Capuano, George; Lu, Wentao; Berry, Pamela; Kane, Thomas; Naylor, Stuart; Georgiou, Michalis; Kalitzeos, Angelos; Ali, Robin R.; Forbes, Alexandria; Bainbridge, James
Source
In American Journal of Ophthalmology September 2023 253:243-251
Subject
Language
ISSN
0002-9394