학술논문
Editing the core region in HPFH deletions alters fetal and adult globin expression for treatment of β-hemoglobinopathies
Document Type
Article
Author
Venkatesan, Vigneshwaran; Christopher, Abisha Crystal; Rhiel, Manuel; Azhagiri, Manoj Kumar K.; Babu, Prathibha; Walavalkar, Kaivalya; Saravanan, Bharath; Andrieux, Geoffroy; Rangaraj, Sumathi; Srinivasan, Saranya; Karuppusamy, Karthik V.; Jacob, Annlin; Bagchi, Abhirup; Pai, Aswin Anand; Nakamura, Yukio; Kurita, Ryo; Balasubramanian, Poonkuzhali; Pai, Rekha; Marepally, Srujan Kumar; Mohankumar, Kumarasamypet Murugesan; Velayudhan, Shaji R.; Boerries, Melanie; Notani, Dimple; Cathomen, Toni; Srivastava, Alok; Thangavel, Saravanabhavan
Source
In Molecular Therapy - Nucleic Acids 13 June 2023 32:671-688
Subject
Language
ISSN
2162-2531