학술논문
Precise correction of a spectrum of β-thalassemia mutations in coding and non-coding regions by base editors
Document Type
Article
Author
Prasad, Kirti; Devaraju, Nivedhitha; George, Anila; Ravi, Nithin Sam; Paul, Joshua; Mahalingam, Gokulnath; Rajendiran, Vignesh; Panigrahi, Lokesh; Venkatesan, Vigneshwaran; Lakhotiya, Kartik; Periyasami, Yogapriya; Pai, Aswin Anand; Nakamura, Yukio; Kurita, Ryo; Balasubramanian, Poonkuzhali; Thangavel, Saravanabhavan; Velayudhan, Shaji R.; Newby, Gregory A.; Marepally, Srujan; Srivastava, Alok; Mohankumar, Kumarasamypet M.
Source
In Molecular Therapy - Nucleic Acids 11 June 2024 35(2)
Subject
Language
ISSN
2162-2531