학술논문
Health-Related Quality of Life Following Valoctocogene Roxaparvovec Gene Therapy for Severe Hemophilia A in the Phase 3 Trial GENEr8-1
Document Type
Abstract
Author
O'Mahony, Brian; Mahlangu, Johnny; Peerlinck, Kathelijne; Wang, Jiaan-Der; Lowe, Gillian; Tan, Chee Wee; Giermasz, Adam; Tran, Huyen A; Khoo, Teh-Liane; Cockrell, Erin; Pepperell, Dominic; Chambost, Hervé; López Fernández, María Fernanda; Kazmi, Rashid; Majerus, Elaine; Skinner, Mark W; Klamroth, Robert; Quinn, Jennifer; Yu, Hua; Wong, Wing Yen; Lawal, Adebayo; Robinson, Tara M; Kim, Benjamin
Source
In Blood 23 November 2021 138 Supplement 1:4916-4916
Subject
Language
ISSN
0006-4971