학술논문
Long-term administration of intravenous Trappsol® Cyclo™ (HP-β-CD) results in clinical benefits and stabilization or slowing of disease progression in patients with Niemann-Pick disease type C1: Results of an international 48-week Phase I/II trial
Document Type
Article
Author
Source
In Molecular Genetics and Metabolism Reports September 2023 36
Subject
Language
ISSN
2214-4269